529 Gene Therapy, RNA & Peptide Therapy Companies - Worldwide

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13therapeutics	OR - Portland	Peptide Therapeutics
4D Molecular Therapeutics	CA - Emeryville	Gene Therapy
A28 Therapeutics	CA - La Jolla	Targeted Lytic Peptides for the Treatment of Cancer
Aanastra	CA - Los Angeles	RNA therapeutics
AAVantgarde Bio	Italy - Milan	AAV-Gene Therapy Platform
AaviGen	Germany - Heidelberg	Precision gene therapies for heart failure
AAVogen	MD - Rockville	Gene therapeutics to strengthen muscle and fight disease
Abeona Therapeutics	OH - Cleveland	Therapies for Sanfilippo (SF) Syndrome Type A and Type B.
Abogen	China - Suzhou	mRNA
AcadeMab Biomedical	Taiwan - Taipei City	Antibody & mRNA Drugs
ACON Pharmaceuticals	NJ - Cranbury	siRNA, LNP
ADARx Pharmaceuticals	CA - San Diego	RNA Therapeutics
Addimmune	MD - Rockville	HIV Gene Therapy
AdipoPharma	France - Strasbourg	Therapeutic Peptide for Diabetes
Adolore BioTherapeutics	FL - Delray Beach	Gene Therapy Analgesic for Pain
Adverum Biotechnologies	CA - Redwood City	Adeno-Associated Virus Delivery, Gene Therapy
Affinia Therapeutics	MA - Waltham	Gene Delivery
Aizen Therapeutics	CA - San Diego	Mirror Peptides
Alcyone Therapeutics	MA - Lowell	Gene Therapy
Aligos Therapeutics	CA - South SF	Therapies for hepatologic diseases and viral infections
Alltrna	MA - Cambridge	tRNA therapies
Allysta Pharmaceuticals	WA - Bellevue	Therapeutic Peptides
Alnylam Pharmaceuticals	MA - Cambridge	RNAi
Alnylam Pharmaceuticals	Switzerland - Zug	RNAi
Alnylam Pharmaceuticals	UK - Maidenhead	RNAi
Alpha-1 Biologics	NY - Stony Brook	Small molecules, peptides, diagnostic, vaccine
Altamira Therapeutics	Bermuda - Hamilton	RNA Therapies
Altamira Therapeutics	DE - Newark	RNA Therapies
Altamira Therapeutics	Switzerland - Basel	RNA Therapies
Altheia Science	Italy - Milan	Cell & Gene Therapy for Autoimmune Disorders
AltPep	WA - Seattle	Alternating Peptides for Neurological Diseases
AlveoGene	UK - Oxford	Inhaled Gene Therapy
Alzamend Neuro	GA - Atlanta	Alzheimer's Treatment
Amarna Therapeutics	Netherlands - Leiden	Viral Gene Delivery Platform
Amaroq Therapeutics	New Zealand - Auckland	lncRNA Therapeutics
Ambulero	FL - Miami	Cell & Gene Therapies
American Gene Technologies	MD - Rockville	Gene Therapy and Immunotherapy Company. Lentiviral Vector Platform and Indication-Specific Technologies. Lead Therapeutics for an HIV Cure, Liver Cancer Cure, and PKU therapy
Ampersand Biomedicines	MA - Boston	AND-Body Therapeutics
Amplo Biotechnology	CA - San Diego	Treatment for congenital myasthenic syndromes
Amyndas Pharmaceuticals	Greece - Glyfada	Peptide for various disorders
Amytrx Therapeutics	AL - Birmingham	Peptide Therapies
Amytrx Therapeutics	TN - Nashville	Peptide Therapies
Animate Biosciences	MA - Cambridge	Peptides for Scar Reduction
Antag Therapeutics	Denmark - Copenhagen	Therapeutic peptides for dietary-related metabolic diseases
Antion Biosciences	Switzerland - Plan-les-Ouates	Gene & Cell Therapy
Apellis Pharmaceuticals	Australia - Hawthorn East	Cyclic peptide analog
Apellis Pharmaceuticals	CA - San Francisco	Cyclic peptide analog
Apellis Pharmaceuticals	Germany - Munich	Cyclic peptide analog
Apellis Pharmaceuticals	MA - Waltham	Cyclic peptide analog
Apellis Pharmaceuticals	Switzerland - Zug	Cyclic peptide analog
APEPTICO	Austria - Vienna	Peptide Drugs
Apertura Gene Therapy	NY - New York	AAV vectors for Gene Therapy
APIM Therapeutics	Norway - Rissa	Peptide Drugs
Aptadir	Italy - Milan	RNA Therapeutics
Aptahem	Sweden - Malmö	Aptamer-based Drugs
aptaTargets	Spain - Madrid	Aptamer Drugs
Arbutus Biopharma	PA - Warminster	RNAi
Arcturus Therapeutics	CA - San Diego	Lipid nanoparticle (LNP) mRNA drug delivery systems
Argo Biopharma	China - Shanghai	siRNA Drugs
Armatus Bio	OH - Columbus	RNAi Therapeutics
Aro Biotherapeutics	PA - Philadelphia	Protein Scaffolds, Antisense Oligonucleotide
Arrowhead Pharmaceuticals	CA - Pasadena	RNAi
Arrowhead Pharmaceuticals	CA - San Diego	RNAi
Arrowhead Pharmaceuticals	WI - Madison	RNAi
Arrowhead Pharmaceuticals	WI - Verona	RNAi
Art Bioscience	Israel - Rehovot	DMD Gene Therapy
Artery Therapeutics	CA - San Ramon	Peptide therapies
ARTHEx Biotech	Spain - Paterna	Antisense RNA Compounds
Ascidian Therapeutics	MA - Boston	Mutated exon replacement
Aspa Therapeutics	CA - Palo Alto	Gene Therapy
Astellas	China - Shenyang	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	IL - Northbrook	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	Ireland - Dublin	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	Ireland - Killorglin	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	Japan - Takahagi	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	Japan - Tokyo	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	Japan - Yaizu	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Aston Sci.	Korea - Seoul	Therapeutic cancer vaccines and proteostasis modulators
Atalanta Therapeutics	MA - Boston	RNAi therapeutics
Atamyo Therapeutics	France - Evry	Gene Therapies targeting neuromuscular diseases
Atorvia Health Technologies	ON - Kanata	Kidney-targeted peptide that prevents regulated cell death and kidney failure
Atsena Therapeutics	NC - Durham	Gene Therapy
Attralus	FL - Naples	Amyloidosis Treatments
Augelux Therapeutics	China - Wuhan	AAV-Based Optogenetic Gene Therapies for Ocular Diseases
Avellino Laboratories	CA - Menlo Park	Gene Therapy, Molecular Diagnostics
Averna Therapeutics	Israel - Ness Ziona	Developing genomic medicines that insert therapeutic genes into safe harbors within the DNA
Averna Therapeutics	MA - Watertown	Developing genomic medicines that insert therapeutic genes into safe harbors within the DNA
AviadoBio	UK - London	Gene Therapies for neurodegenerative
Avidity Biosciences	CA - San Diego	Antibody-Oligonucleotide Conjugates
Avilex Pharma	Denmark - Copenhagen	Peptide for ischemic stroke
Avista Therapeutics	PA - Pittsburgh	Gene Therapy Delivery
Avrion Therapeutics	Switzerland - Lausanne	Gene Therapies for Neurodegenerative Diseases
Avstera Therapeutics	PA - Malvern	Cell Therapy, Cancer Vaccine, mRNA
Axoltis Pharma	France - Lyon	Neurological Peptide Drugs
Axovia Therapeutics	UK - London	AAV Gene Therapy
Basking Biosciences	OH - Columbus	Reversible thrombolytic therapy for acute ischemic stroke
BDgene Therapeutics	China - Shanghai	mRNA-based CRISPR editing components
Beacon Therapeutics	MA - Cambridge	Gene Therapy
Beacon Therapeutics	UK - London	Gene Therapy
Bedrock Therapeutics	NC - Chapel Hill	AAV Research and Development Gene Therapy
Belief BioMed	China - Shanghai	AAV-delivered Gene Therapies
Benitec Biopharma	CA - Hayward	DdRNAi
Bicycle Therapeutics	MA - Cambridge	Peptides
Bicycle Therapeutics	UK - Cambridge	Peptides
Bio-Path Holdings	TX - Bellaire	Antisense DNA therapeutics
BioGene Therapeutics	TX - Austin	Bioresponsive lipid nanoparticle technology and innovative gene therapy
Biogenera	Italy - Ozzano dell'Emilia	DNA Oligonucleotide Therapies
Biointaxis	Spain - Barcelona	Gene Therapy for Friedreich Ataxia
Biojo Sciences	Korea - Seoul	Gene Therapy & Others
Biojo Sciences	MD - Bethesda	Gene Therapy & Others
Biomonadic	CA - Berkeley	Klotho Gene Therapy
Bionic Sight	NY - New York	Blindness Treatment Gene Therapy and Device
BioNTech	CA - San Diego	mRNA, Vaccines, Biologics
BioNTech	Germany - Berlin	mRNA, Vaccines, Biologics
BioNTech	Germany - Idar-Oberstein	mRNA, Vaccines, Biologics
BioNTech	Germany - Mainz	mRNA, Vaccines, Biologics
BioNTech	MA - Cambridge	mRNA, Vaccines, Biologics
BioNTech	MD - Gaithersburg	mRNA, Vaccines, Biologics
Biorchestra	Korea - Daejeon	Novel RNA-based Therapeutics
Biorchestra	MA - Cambridge	Novel RNA-based Therapeutics
Biosortia Pharmaceuticals	OH - Columbus	Peptide Drugs
Biosyngen	Singapore - Singapore	Cell & Gene Therapy, Antibodies
BioViva Science	WA - Bainbridge Island	Gene Therapy Delivery
Black Swan Pharmaceuticals	NC - Wake Forest	Antisense RNA-based therapeutics for ALS
BlackfinBio	UK - Cheshire	Gene Therapy
Bolden Therapeutics	RI - Providence	Antisense Oligonucleotides for Neuro Indications
Borealis Biosciences	BC - Vancouver	RNA Medicine for Kidney Disease
BreezeBio	CA - Brisbane	Nonviral CRISPR-delivery system
BrightPath Biotherapeutics	Japan - Tokyo	Peptide Therapies
BRIM Biotechnology	Taiwan - Taipei	Peptides, Recombinant Proteins
Brink Therapeutics	France - Paris	Programmable recombinases
BRL Medicine	China - Shanghai	Cell & Gene Therapy Platforms
Broken String Biosciences	UK - Cambridge	Gene Edited Cell & Gene Therapy
C -Biomex	Korea - Pohang	Radionuclides, peptide
Capacity Bio	CA - Los Angeles	Mitophagy
Capsida Biotherapeutics	CA - Thousand Oaks	AAV Gene Therapy
Carbon Biosciences	MA - Waltham	Gene Therapy
Cardior Pharmaceuticals	Germany - Hanover	Non-coding RNA based therapeutics
Caregen Biopharma	Korea - Anyang	Growth Factors & Biomimetic Peptides
Carmine Therapeutics	Singapore - Singapore	Medicines based on red blood cell extracellular vesicles (RBCEVs), for the delivery of novel therapeutic modalities that include nucleic acids
Causeway Therapeutics	UK - Glasgow	microRNA
Cell BioEngines	NY - New York	Cell-based Immunotherapies
Cellastra	CA - San Francisco	Anti-scarring gene therapy/peptides
CellGenTech	Japan - Chiba	Ex-Vivo Gene Therapy
Celosia Therapeutics	Australia - Sydney	Neurodegenerative Therapies
Ceria Therapeutics	AZ - Tucson	mRNA Delivery
Channavix Therapeutics	NY - Pittsford	Non-opioid analgesics
Chimerna Therapeutics	NY - New York	RNA Therapeutics
Chimeron Bio	PA - Philadelphia	Cancer Immunotherapy
Chrysalis BioTherapeutics	TX - Galveston	Peptide to stimulate tissue regeneration
Circle Pharma	CA - South SF	Macrocyclic Therapeutics
CircNova	MI - Detroit	Circular RNA
CirCode Biomed	China - Shanghai	RNA Therapeutics
City Therapeutics	MA - Cambridge	RNAi Therapies
CiVi Biopharma	MD - Chevy Chase	Novel therapies against cardiometabolic diseases
CLOVERNA	Japan - Okayama	RNA Targeting Oligonucleotides
Coave Therapeutics	France - Paris	Gene Therapy in Ophthalmology
Code Biotherapeutics	PA - Hatfield	DNA-based Gene Therapy Vector

Codone Biotechnology	China - Shanghai	tRNA Therapies
Coegin Pharma	Sweden - Lund	Inflammatory Targeting, Small Molecules & Peptides
Comanche Biopharma	MA - Concord	siRNA for Preeclampsia
Complement Therapeutics	UK - London	Complement Medicines - AAV Gene Therapy, Biologics
Concinnity Genetics	UK - Glasgow	RNA-control of gene therapies
Constant Therapeutics	MA - Boston	Peptide Treatments
Corsera Health	MA - Boston	RNAi Therapeutics for Cardiovascular
Courage Therapeutics	MA - Newton	Eating Disorder Treatments
Crane Biosciences	UK - London	Gene Therapies
Creyon Bio	CA - Carlsbad	Oligonucleotide-based Medicines
CureGenetics	China - Suzhou	Gene-editing - Diagnostics, Therapies
CuroNZ	New Zealand - Hamilton	Neural Regeneration Peptides
Cytovation	Norway - Bergen	Peptide for cancer
Cytovation	UK - London	Peptide for cancer
Deep Genomics	ON - Toronto	AI-discovery, Oligonucleotide Therapies
Diapin Therapeutics	MI - Ann Arbor	Peptide for diabetes
DiNAQOR	CA - Laguna Hills	Gene Therapy for Heart Conditions
DiNAQOR	Germany - Hamburg	Gene Therapy for Heart Conditions
DiNAQOR	Switzerland - Schlieren	Gene Therapy for Heart Conditions
Diorasis Therapeutics	MA - Boston	Gene Therapy for Glaucoma
Dydo Pharma	Japan - Osaka	Small Molecules, Gene Therapy
Dynavax Technologies	CA - Emeryville	Synthetic oligonucleotides vaccines, adjuvants
E-Star BioTech	UT - Salt Lake City	Peptide Therapies
EA Pharma	Japan - Tokyo	Amino Acid Treatments
East Ocyon Bio	India - Gurgaon	NK Cells, Gene Therapy
EG 427	France - Paris	Pinpoint Gene Therapy
Eldec Pharmaceuticals	NC - Durham	Peptide Therapies
Eleven Therapeutics	Israel - Tel Aviv	Small interfering RNAs with ultra-long durability by utilizing high throughput combinatorial chemistry and AI
Eleven Therapeutics	UK - Cambridge	Small interfering RNAs with ultra-long durability by utilizing high throughput combinatorial chemistry and AI
Eli Lilly	CA - San Diego	Biologics Discovery
Eli Lilly	France - Neuilly-sur-Seine	Small Molecules, Biologics
Eli Lilly	IN - Indianapolis	Small Molecules, Biologics
Eli Lilly	Ireland - Kinsale	Small Molecules, Biologics
Eli Lilly	Italy - Sesto Fiorentino	Small Molecules, Biologics
Eli Lilly	MA - Boston	Small Molecules, Biologics
Eli Lilly	Mexico - San José	Small Molecules, Biologics
Eli Lilly	PR - Carolina	Recombinant Insulin
Eli Lilly	PR - Mayaguez	Small Molecules, Biologics
Eli Lilly	Spain - Alcobendas	Small Molecules, Biologics
Eli Lilly	UK - Basingstoke	Small Molecules, Biologics
Elicera Therapeutics	Sweden - Gothenburg	Cell & Gene Therapy Immuno-Oncology
Elpida Therapeutics	CA - Encino	Gene Therapy for Rare Disease
Emmaus Life Sciences	CA - Torrance	Oral amino acid treatment
Encoded Therapeutics	CA - South SF	Gene Therapy
Endsulin	WI - Madison	Genetic therapy for type 1 diabetes
Engage Bio	CA - San Carlos	Tethosome Gene Therapy
Envoya	MA - Boston	Gene Therapy
EOM Pharmaceuticals	NJ - Montvale	Peptide-nucleic Acid Solutions
Epics Therapeutics	Belgium - Gosselies	RNA Therapies
EpilepsyGTx	UK - Waterbeach	Epilepsy Gene Therapy
Epsilon Molecular Engineering	Japan - Saitama	Heavy chain single domain antibodies
Esperovax	MI - Plymouth	Targeted Oral mRNA
Esteve	Spain - Barcelona	Small Molecules, Gene Therapy
Ethris	Germany - Planegg	MRNA-based therapies, vaccines
ExCellThera	QC - Montréal	Growing blood stem cells for therapeutic use
ExcepGen	CA - San Francisco	RNA Therapeutics Platform
Excision BioTherapeutics	CA - San Francisco	Gene Editing
Exegenesis Bio	China - Hangzhou	Gene Therapy
Exegenesis Bio	MA - Lexington	Gene Therapy
Exegenesis Bio	PA - Horsham	Gene Therapy
Expression Therapeutics	GA - Tucker	Gene Therapies
Feldan Therapeutics	QC - Quebec City	Peptide-based Intracellular Delivery Technology
Fennec Pharmaceuticals	NC - Durham	Small Molecules, Cyclic Peptides
Find Therapeutics	QC - Saint-Laurent	GPCR-Targeting Therapeutics
Flamingo Therapeutics	Belgium - Leuven	RNA Therapeutics
Flashpoint Therapeutics	IL - Chicago	Nanoscale design of therapeutic architecture to optimize anti-cancer immune response
Fractyl Health	MA - Burlington	Thermal ablation therapy, Gene Therapy
Frontera Therapeutics	China - Suzhou	Gene Therapy Development
Frontera Therapeutics	MA - Bedford	Gene Therapy Development
Fuse Vectors	Denmark - Copenhagen	Gene Therapy Vectors
GEMMA Biotherapeutics	PA - Philadelphia	Gene Therapy
Gemvax & KAEL	Korea - Seongnam	Peptide Immunotherapy
Genascence	CA - Palo Alto	Musculoskeletal Gene Therapies
Geneos Therapeutics	PA - Philadelphia	Plasmid-based Neoantigen-targeted Cancer Therapies
Genervon Biopharmaceuticals	CA - Pasadena	Synthetic Peptide
Genespire	Italy - Milan	Gene Therapy
Genetix Biotherapeutics	MA - Somerville	Gene Therapy, Cellular Extraction & Reintroduction
GeneVentiv Therapeutics	NC - Raleigh	Gene Therapy
Genexine	Korea - Seoul	Biologics, DNA Plasmid Vaccine
Genflow Biosciences	Belgium - Charleroi	Anti-aging Gene Therapy
Genflow Biosciences	UK - London	Anti-aging Gene Therapy
GenKOre	Korea - Daejeon	Gene-editing therapies
GenKOre	Korea - Seoul	Gene-editing therapies
Genocury Biotech	China - Shenzhen	Off-the-shelf Cell & Gene Therapy
Genosera	OH - Columbus	Gene Therapy
Genprex	TX - Austin	Non Viral Gene Delivery
GenSight Biologics	France - Paris	Ophthalmic Gene Therapy
GenVivo	CA - San Marino	Proprietary Gene Delivery Technology
GlioCure	France - Angers	Peptide
Grace Science	CA - Menlo Park	Therapies based on the function of NGLY1, AAV gene therapy, small molecules
Gradalis	TX - Carrollton	Cancer immunotherapy, RNAi
Gritgen Therapeutics	China - Suzhou	Gene Therapy
Guardian Therapeutics	MA - Lexington	Aptamer Therapeutics
Harness Therapeutics	UK - Cambridge	IncRNA
HAYA Therapeutics	CA - San Diego	RNA-based, RNA-targeting Fibrotic Therapies
HAYA Therapeutics	Switzerland - Lausanne	RNA-based, RNA-targeting Fibrotic Therapies
Helix Nanotechnologies	MA - Boston	DNA Therapy
Helixmith	Korea - Seoul	plasmid DNA based gene therapy
Henovcom Bioscience	China - Guangzhou	Small Molecules, mRNA, 505 (b)(2)
Heqet Therapeutics	Italy - Turin	Noncoding RNA as Therapeutic
Highlight Therapeutics	Spain - Valencia	Immuno-oncology, synthetic dsRNA complex
HitGen	China - Chengdu	DNA encoded library for drug discovery
Holostem Tarapie Avanzate	Italy - Modena	Cell & Gene Therapy
Hubble Therapeutics	NH - Hanover	Gene therapy for Leber Congenital Amaurosis Type 16
HuidaGene Therapeutics	China - Shanghai	Gene Therapy, Gene editing platform, delivery vector platform
Hunterian Medicine	MA - Cambridge	CRISPR-based drug discovery
Hybridize Therapeutics	Netherlands - Oegstgeest	RNA treatments for kidney disease
Ibex Biosciences	MD - Cumberland	Biologics, Cell Therapy, Gene Therapy
iCell Gene Therapeutics	NY - Stony Brook	Gene Therapy for Cancer
Ikarovec	UK - Norwich	Ocular Gene Therapy
ILC Therapeutics	UK - Glasgow	Synthetic Peptides
Immorna Biotherapeutics	China - Shanghai	Self-Replicating RNA
Immuno Cure Biotech	China - Hong Kong	Therapeutic Antibodies, DNA Vaccines
ImmunoVec	CA - Los Angeles	Gene Therapy for Hematopoietic Diseases
Imugene	Australia - Sydney	Peptide immunotherapy
Innovac Therapeutics	MA - Cambridge	RNA Therapeutics
InnoVec Biotherapeutics	China - Beijing	AAV-Based Gene Therapy
Inomagen Therapeutics	IL - Chicago	Gene Therapies for Atrial Fibrillation
Inotrem	France - Paris	Peptide Therapy
Inotrem	France - Vandoeuvre	Peptide Therapy
Inovio Pharmaceuticals	CA - San Diego	DNA Vaccines
Inovio Pharmaceuticals	PA - Plymouth Meeting	DNA Vaccines
Interius BioTherapeutics	PA - Philadelphia	Novel methods for in vivo cell-specific gene delivery
InterK Peptide Therapeutics	Australia - Lane Cove West	Synthetic Peptides to Treat Cancer
Invectys	France - Paris	DNA Vaccine
invIOs	Austria - Vienna	Novel cancer immunotherapies, cell, siRNA, peptides
Ionis Pharmaceuticals	CA - Carlsbad	RNA
Jaguar Gene Therapy	IL - Lake Forest	AAV-Based Gene Therapies
Jaya Biosciences	CA - South SF	CNS-directed gene therapies
Jaya Biosciences	NC - Chapel Hill	CNS-directed gene therapies
Judo Bio	MA - Cambridge	Oligonucleotide Therapies Delivered to Kidney
Junevity	CA - San Francisco	Long-lasting siRNA Therapies
Juniper Biologics	Singapore - Singapore	Small Molecules, Cell Therapy, Gene Therapy
Kailera Therapeutics	CA - San Diego	Peptides, Small Molecules
Kailera Therapeutics	MA - Waltham	Peptides, Small Molecules
Kairos Pharma	CA - Los Angeles	Cell Therapy, Antibodies, Small Molecules
Kanglin Biotechnology	China - Hangzhou	AAV Gene Therapy, Stem Cell Platform
Kelonia Therapeutics	MA - Boston	in vivo CAR T Gene Therapy
Kerna Labs	CA - San Francisco	AI and high-throughput biology - RNA therapeutics
Kinea Bio	WA - Seattle	Gene Therapy for Muscle Disease
Kither Biotech	Italy - Torino	Therapies for the treatment of rare pulmonary diseases
Kolon Life Science	Korea - Seoul	Cell & Gene Therapy, APIs
Korro Bio	MA - Cambridge	RNA-editing Drugs
Kriya Therapeutics	CA - Redwood City	Gene Therapy
Kriya Therapeutics	NC - Morrisville	Gene Therapy
Krystal Biotech	PA - Pittsburgh	Gene Therapy
Lactocore	Germany - Berlin	CNS Peptides
Lactocore	MA - Newton	CNS Peptides
Ladder Bio	PA - Blue Bell	Spiroligomers
Lassogen	CA - San Diego	Lasso peptide-based therapies
Lateral Pharma	Australia - Melbourne	Repurposed Peptide
Leal Therapeutics	MA - Worcester	CNS Therapies
Lexeo Therapeutics	NY - New York	Gene Therapy
Ligandal	NY - Long Island City	Nanomedicine delivery for Genetic Medicines
Longevity Biotech	PA - Philadelphia	Synthetic Peptides
Loto Biotech	Italy - L'Aquilo	siRNA Therapies
Luxna Biotech	Japan - Osaka	Oligonucleotide Therapeutics
Lytica Therapeutics	MA - Cambridge	Antimicrobial peptide Design
Lytix Biopharma	Norway - Oslo	Oncolytic Peptide

Mach5 Therapeutics	GA - Atlanta	Gene therapies and advanced biologics
Mahzi Therapeutics	CA - San Mateo	Gene therapy for rare genetic neurodevelopmental disorders
MAIA Biotechnology	IL - Chicago	Peptide Cancer Therapies
MalarVx	WA - Seattle	Malaria Vaccine
Mammoth Biosciences	CA - Brisbane	CRISPR, Gene-Editing Therapies
Matrix Biomed	CA - Irvine	Gene therapy for various cancers
Maze Therapeutics	CA - South SF	Small Molecules, Gene Therapy, Antisense Oligonucleotides, Biologics
MBX Biosciences	IN - Carmel	Hormone Analogues for Rare Endocrine Diseases
MDimune	Korea - Seoul	Drug Delivery Based on Cell-Derived Vesicles
Medera	MA - Boston	Cell & Gene Therapies
Medikine	CA - San Diego	Small Molecules, Peptide
Medley Therapeutics	TX - Houston	Genetic medicines that regenerate tissue and repair organs
MeiraGTx	UK - London	Gene Therapy
Merlin Biotech	PA - Doylestown	RNA Technology
MimiVax	NY - Buffalo	Immunotherapeutics
MiNA Therapeutics	UK - London	Small activating RNA
MindMaze Therapeutics	Switzerland - Geneva	Peptide & Protein Therapies
miRecule	MD - Gaithersburg	microRNA Therapeutics for Cancer
Mitotherapeutix	CT - Farmington	siRNA drugs
Modalis Therapeutics	Japan - Tokyo	Genome Editing Tools for Therapeutic Discovery
Modalis Therapeutics	MA - Waltham	Genome Editing Tools for Therapeutic Discovery
Moderna Therapeutics	Australia - Melbourne	RNA Therapies
Moderna Therapeutics	MA - Cambridge	RNA Therapies
Moderna Therapeutics	MA - Cambridge	RNA Therapies
Moderna Therapeutics	MA - Norwood	RNA Therapies
Moderna Therapeutics	UK - Harwell	RNA Therapies
Momotaro-Gene	Japan - Okayama	Cancer Gene Therapy
Mustang Bio	MA - Worcester	Immunotherapies
MyoPax	Germany - Berlin	Cell & Gene Therapies
Myosana Therapeutics	WA - Seattle	Non-viral Gene Therapy
Myrtelle	MA - Wakefield	Gene Therapy
NanoCell Therapeutics	PA - Berwyn	Gene Therapy
Nanogenics	UK - Selkirk	Gene Therapy
Nanoscope Therapeutics	TX - Dallas	AAV-delivered opsin
NapaJen Pharma	Japan - Tokyo	Oligonucleotide Drugs
NapaJen Pharma	WA - Seattle	Oligonucleotide Drugs
Navega Therapeutics	CA - San Diego	Chronic Pain Treatment
NeoMatrix Therapeutics	NY - Stony Brook	Bioactive Peptides for Burn Healing
Nephrogen	NY - New York	Gene Therapy for Kidney Disease
NervGen Pharma	BC - Vancouver	Peptide inhibitor of protein tyrosine phosphatase sigma
NeuExcell Therapeutics	PA - Philadelphia	Gene Therapy for Neural Regeneration & Repair
Neumirna	Denmark - Copenhagen	RNA Therapeutics
Neurexis Therapeutics	CO - Aurora	Peptide for Cardiac Indications
Neurogene	NY - New York	Genetic Therapies
Neurogene	TX - Houston	Genetic Therapies
NeuroGT	NC - Chapel Hill	Patient-centric Gene Therapy
Neurophth Therapeutics	China - Wuhan	Ophthalmology Gene Therapy
NeuroQure	CA - Dana Point	Gene Therapy for Neurological Disorders
Neuroscientific Biopharmaceuticals	Australia - Cottesloe	Peptide for neurological treatments
Neurotez	NJ - Jersey City	Peptide Treatment for Alzheimer's
NeuShen Therapeutics	China - Shanghai	AAV Gene Therapy, Small Molecules
NGGT	CA - Walnut Creek	Gene Therapies
Nitto BioPharma	CA - San Diego	Drug Delivery of siRNA
Novartis	MA - Cambridge	Small Molecules, Vaccines, Biologics / Diagnostics
Novartis	Mexico - Mexico City	Small Molecules, Vaccines, Biologics
Novartis	NJ - East Hanover	Small Molecules, Vaccines, Biologics
Novartis	Switzerland - Basel	Small Molecules, Vaccines, Biologics
Nuevocor	Singapore - Singapore	AAV-based gene therapy
Nuntius Therapeutics	UK - London	mRNA Therapies
Nuravax	CA - Irvine	DNA Vaccine
Nuvie Bio	CA - San Diego	peptide therapy targeting calcitonin gene-related peptide receptor
Nykode Therapeutics	Norway - Oslo	Therapeutic DNA Vaccine
NysnoBio	CA - Mill Valley	Parkin protein therapeutics
Obsidian Therapeutics	MA - Cambridge	Cell & Gene Therapies
Ochre Bio	UK - Oxford	siRNA liver drugs
Oculgen	China - Shenzhen	Gene and cell therapies, biologics, vaccines
Oculogenex	CA - La Habra	Gene Therapy for Vision
Odimma Therapeutics	France - Strasbourg	Personalized Cancer Immunotherapy
OliPass	Korea - Gyeonggi	Peptide nucleic acid derivatives
OliX Pharmaceuticals	Korea - Seongnam	RNAi Treatments
Oncogenuity	FL - Bay Harbor Islands	Oligonucleotide platform for the treatment of genetically driven cancers
Oncolyze	NY - New York	Peptide Therapy
Oncotherapy Science	Japan - Kawasaki	Small Molecule, peptides, antibody therapies, contract analytical
Oncovir	DC - Washington	dsRNA viral mimic
ONL Therapeutics	MI - Ann Arbor	Small molecule peptide
Onodera	Japan - Kanagawa	Gene Therapy
Opus Genetics	NC - Raleigh	Ophthalmology Gene Therapy
Orbital Therapeutics	MA - Cambridge	RNA technology (not RNAi)
Orchard Therapeutics	MA - Boston	Ex-vivo autologous hematopoietic stem cell gene therapy
Orchard Therapeutics	UK - London	Ex-vivo autologous hematopoietic stem cell gene therapy
Orna Therapeutics	MA - Watertown	oRNA, Delivery
OrthoTrophix	CA - Foster City	Bone, cartilage and teeth therapies
Oryn Therapeutics	CA - West Hollywood	Macrocyclic peptide therapeutics
Oryx Translational Medicine	Germany - Vaterstetten	Cancer Immunotherapy
Oxalo Therapeutics	IL - Chicago	Peptide-based therapeutics to treat rare renal diseases and prevent recurrent kidney stones
Pantherna Therapeutics	Germany - Hennigsdorf	Nanoparticle Delivery for mRNA drugs
ParcelBio	CA - San Francisco	Next-generation mRNA medicines
Passage Bio	PA - Philadelphia	Gene Therapy
PCI Biotech	Norway - Oslo	Drug Delivery
PEEL Therapeutics	UT - Salt Lake City	Nature-inspired Cancer Therapies
PEP-Therapy	France - Paris	Peptide Therapies
PepKon	France - Louveciennes	Peptide Therapies for Cancer
Peptilogics	PA - Pittsburgh	Peptide Therapeutics
Peptinov	France - Paris	Peptide-based active immunotherapy
Peptomyc	Spain - Barcelona	Cell Penetrating Peptides
Peptron	Korea - Daejeon	Peptide-based Medicine Platform
Peroxitech	PA - Philadelphia	Peptide treatment for acute lung injury
Pfizer	CA - La Jolla	Peptides, Monoclonal Antibodies
Pfizer	NC - Durham	Small Molecules, Vaccines, Biologics
Pfizer	WA - Bothell	Small Molecules, Vaccines, Biologics
Phaim Pharma	UK - London	Peptide Diabetes Treatment
PharmaIN	WA - Bothell	Subcutaneous peptides, Out licensing
Phinomics	CA - San Carlos	Circular DNA
Phio Pharmaceuticals	PA - King of Prussia	RNAi
Phlox Therapeutics	Netherlands - Naarden	Gene Therapy for Heart Disease
Phoenix Nest	NY - Brooklyn	Sanfilippo syndrome treatment
Phylex BioSciences	CA - Del Mar	Vaccines
Pinion Immunotherapeutics	MD - North Bethesda	mRNA Vaccine Technology
PinotBio	Korea - Suwon	Small molecules, ADC, Nucleoside-based Therapy
Plasticell	UK - Stevenage	Cell, Gene Therapy, Blood Products
Poolbeg Pharma	UK - London	Developing drugs to sell off
Precigen	MD - Germantown	Cell & Gene Therapy
Prevail Therapeutics	NY - New York	AAV-based gene therapies
Priavoid	Germany - Düsseldorf	All-d-peptides
Primera Therapeutics	US - Virtual	mtDNA engineering toolbox for mitochondrial diseases
Prolifagen Therapeutics	PA - Doylestown	microRNA
ProQR Therapeutics	MA - Cambridge	Oligonucleotide Therapy
ProQR Therapeutics	Netherlands - Leiden	Oligonucleotide Therapy
Protagenic Therapeutics	NY - New York	Neuro-Active Peptides
Protagonist Therapeutics	Australia - Brisbane	Oral peptides
Protagonist Therapeutics	CA - Newark	Oral peptides for GI indications
Protelight Pharmaceuticals	China - Jiangyin	Peptide and Small Molecules Therapies
ProtoKinetix	OH - Dalton	Anti-aging Glycopeptide
Providence Therapeutics	AB - Calgary	mRNA Cancer Vaccines
PTC Therapeutics	NJ - Warren	Small Molecules, Gene Therapy
PulseSight Therapeutics	France - Paris	Ophthalmic Treatment Plasmid
Purespring Therapeutics	UK - London	Gene Therapy for Kidney Disease
PURMX Therapeutics	Japan - Hiroshima	Nucleic Acid Drugs
PYC Therapeutics	Australia - Nedlands	Peptide drug discovery
Ractigen Therapeutics	China - Nantong	Small activating RNA
Radar Therapeutics	-	Smart Programmable Medicines Using Molecular RNA Sensors
Radella Pharmaceuticals	UK - Aberdeen	Peptide Therapy
Ray Therapeutics	CA - Berkeley	Optogenetic Gene Therapy
ReAlta Life Sciences	VA - Norfolk	Complement and Inflammation Inhibition drug products
Recbio Technology	China - Taizhou	mRNA Covid Vaccine
ReCode Therapeutics	CA - Menlo Park	Nucleic Acid Therapeutic Delivery
Regel Therapeutics	CA - Berkeley	AAV gene delivery
Regel Therapeutics	MA - Cambridge	AAV gene delivery
RegeneRx Biopharmaceuticals	MD - Rockville	Peptides
ReGenTree	NJ - Princeton	Therapeutic Peptides
ReGenX Biosciences	MD - Rockville	Gene Therapy, Biologics
Regenxbio	MD - Rockville	Gene Therapy
Rein Therapeutics	TX - Austin	Perpetually Active Peptides
Rejuve Therapeutics	MD - Beltsville	Gene therapy drug development company researching senescent cell solutions.
Rejuvenate Bio	CA - San Diego	Gene Therapy for Aging
Rejuvenate Biomed	Belgium - Diepenbeek	Combination Drugs for Aging
Rejuvenation Technologies	CA - Mountain View	Telomere Extension via Nucleoside-modified TERT mRNA
Remedium Bio	MA - Needham	Gene Therapy
Renbio	NY - Long Island City	Gene Therapy Directing Antibody Creation in vivo
Renova Therapeutics	CA - Carlsbad	Gene Therapies
Repertoire Immune Medicines	MA - Cambridge	Cell & Peptide-Based Therapies
Replay	CA - San Diego	HSV Vector Gene Therapies
Replicate Bioscience	CA - San Diego	Preventing oncology drug resistance
Replicor	QC - Montréal	DNA, polymer, small molecule combination Hepatitis B treatment
ResoTher Pharma	Denmark - Holte	Cardiovascular Treatment
ResQ Biotech	Greece - Patra	Therapies for Protein Misfolding Diseases
Restore Vision	Japan - Tokyo	Gene Therapy for Blindness due to Retinal Disorders
RheumaGen	CO - Aurora	Cell & Gene Therapy
RhyGaze	Switzerland - Basel	Gene Therapy Targeting Cone Cells

Rhythm Pharmaceuticals	MA - Boston	Peptide Therapeutics
Ribocure Pharmaceuticals	Sweden - Mölndal	RNA Therapeutics
Ribomic	Japan - Tokyo	Aptamers
RiboX Therapeutics	China - Shanghai	Circular RNA
RIGImmune	CT - Farmington	RNA Immunotherapeutics
RinuaGene Biotechnology	China - Suzhou	mRNA Therapies
Riptide Bioscience	CA - Vallejo	Peptide Therapeutics
Risen Pharma Tech	China - Shanghai	Small Molecules, siRNA, Combination Therapies
Risen Pharma Tech	China - Suzhou	Small Molecules, siRNA, Combination Therapies
Rithim Biologics	MD - Woodbine	Gene Therapy for Tachycardias
RNAimmune	MD - Germantown	mRNA therapies
RNatives	Finland - Kuopio	RNA-based gene regulating therapies
Rocket Pharmaceuticals	NJ - Cranbury	Gene Therapies
Rona Therapeutics	China - Shanghai	RNA Therapeutics Platform
RosVivo Therapeutics	NV - Reno	miRNA & siRNA Therapies
Rznomics	Korea - Seongnam	RNA Therapy Platform
Sagittarius Bio	CA - Thousand Oaks	Gene Therapy for Cancer
San Rocco Therapeutics	FL - Tampa	Gene Therapy, Orphan Diseases
Sana Biotechnology	WA - Seattle	Cell & Gene Therapies
SanegeneBio	MA - Woburn	siRNA Drug Discovery
Sapience Therapeutics	NY - Tarrytown	Peptide-based Therapies for cancers
Sapu BioScience	CA - San Diego	RNA & Small Molecule Immuno-oncology Therapies
Sardocor	MA - Boston	Gene therapy
Sciwind Biosciences	China - Hangzhou	Oral peptide delivery
Scopus BioPharma	NY - New York	Immuno-oncology Gene Therapy
Secarna Pharmaceuticals	Germany - Planegg	Antisense Oligonucleotide Therapies
Senisca	UK - Exeter	Antisense Oligonucleotides for Senescence
Senti Biosciences	CA - South SF	Gene Circuits; Cell & Gene Therapies
Sentia Medical Sciences	CA - San Diego	Novel peptide therapeutics
Seragon Biosciences	CA - Irvine	Small Molecules, Gene Therapy
Serodus	Norway - Oslo	Drug Development
Serpin Pharma	VA - Manassas	Peptide drugs
Shape Therapeutics	WA - Seattle	RNA-editing gene therapy
Shenogen Pharma	China - Beijing	Small Molecules, Biologics, Viral
Silence Therapeutics	Germany - Berlin	RNAi
Silence Therapeutics	NJ - Hoboken	RNAi
Silence Therapeutics	UK - London	RNAi
SineuGene	China - Beijing	Gene Therapy
Siren Biotechnology	CA - San Francisco	AAV Immuno-Gene Therapy
Sirius Therapeutics	CA - San Diego	RNAi Therapies
Sirius Therapeutics	China - Shanghai	RNAi Therapies
siRNAgen	Korea - ZZ	siRNA Therapeutics
Sirnaomics	China - Suzhou	RNAi Therapeutics
Sirnaomics	MD - Germantown	RNAi Therapeutics
SiSaf	UK - Guildford	RNA Therapies for Rare Diseases
Skip Therapeutics	Israel - Ness Ziona	RNA-based therapies for rare genetic disorders and common diseases
Skylark Bio	MA - Cambridge	Gene Therapy for Hearing Disorders
SNIPR BIOME	Denmark - Copenhagen	CRISPR for microbiome management, genetically-modified bacteriophages
SOLA Biosciences	MA - Natick	Gene Therapies for Protein Misfolding Diseases
Solid Biosciences	MA - Charlestown	Gene Therapy, Devices, Biologics, Small Molecules all for DMD
Somagenetix	Switzerland - Altendorf	Gene therapy for phagocytic disorders
Soricimed Biopharma	NB - Moncton	Proprietary TRPV6-targeting peptide platform
Sovargen	Korea - Daejeon	RNA therapeutics
Sovargen	Korea - Seoul	RNA therapeutics
SparingVision	France - Paris	Retinal Gene Therapy Treatments
SparingVision	MA - Boston	Retinal Gene Therapy Treatments
Spine BioPharma	NY - New York	Amino acid peptide for spinal pain relief
Spirovant Sciences	PA - Philadelphia	Gene Therapy - Lung Diseases
Splash Pharmaceuticals	CA - San Diego	Peptide
SpliceBio	Spain - Barcelona	Intein Technologies - Gene Therapy
SpliSense	Israel - Jerusalem	Antisense Oligonucleotides
Spur Therapeutics	UK - Stevenage	Protein replacement via Gene Therapy
SRTD biotech	Germany - Jülich	seRNA
Starna Therapeutics	China - Suzhou	mRNA vaccine, therapies
StemCardia	CA - Sacramento	Cell & gene therapies engineered to repair the heart
Sterna Biologicals & KG	Germany - Marburg	Antisense Molecule - DNAzyme
Stoke Therapeutics	MA - Bedford	Antisense Oligonucleotide Medicines
Strand Therapeutics	MA - Boston	Gene Therapy
STRM.BIO	MA - Cambridge	Extracellular vesicles (EVs) to deliver gene therapies
Stylus Medicine	MA - Cambridge	Enzymatic Gene Therapy
Suzhou Ribo Life Science Company	China - Kunshan	RNAi
Switch Therapeutics	CA - South SF	RNAi Therapies
Sylentis	Spain - Madrid	RNAi Treatments
SynaptixBio	UK - Oxford	Development for treatment of severe leukodystrophies, ASO
SYNG Pharmaceuticals	ON - Kingston	Diagnostic, Peptide-based Non-Hormonal Treatment for Endometriosis
SYTE.bio	MA - Boston	Precision therapeutics using its proprietary Linear DNA and Circular RNA technology platforms
TAGCyx Biotechnologies	Japan - Tokyo	Oligonucleotide Drug Discovery Platform
Takara Bio	Japan - Shiga	Gene Therapy, Agribiotech, Biotech Lab Technology
Taysha Gene Therapies	TX - Dallas	Adeno-associated virus gene therapies
TeamedOn	MD - Rockville	Gene therapies for rare ocular diseases
Telocyte	MI - Grand Rapids	Telomerase Therapy for Alzheimer's
Temple Therapeutics	Netherlands - Geleen	Amino Acid-based Surgical Treatment
Tenaya Therapeutics	CA - South SF	Cardiovascular Therapeutics
Tern Therapeutics	DC - Washington	Gene Therapy for Batten Disease
Tetraneuron	Spain - Madrid	Gene Therapy
Tevard Biosciences	MA - Boston	tRNA-based Gene Therapies
Theragene Pharmaceuticals	CA - San Diego	Immunotherapy, gene therapy and peptide delivery
Therorna	China - Beijing	RNA Therapies
Thylacine Biosciences	FL - Miami	engineered antiviral peptides
TME Therapeutics	Japan - Tokyo	dsRNA Treatment for Cancer
Torque Bio	NC - Durham	Gene Therapies
Trace Neuroscience	CA - South SF	Medicines to restore UNC13A function
TransCode Therapeutics	MA - Newton	RNA Delivery, Small Molecule
Transgene	France - Illkirch-Graffenstaden	Viral Vector Therapeutics, Gene Therapy
Transgene	MA - Boston	Viral Vector Therapeutics, Gene Therapy
Translation-X	Switzerland - Basel	Autism Therapies
Treeway	Netherlands - Tilburg	Small Molecules, Gene Therapy
TuHURA Biosciences	FL - Tampa	Cancer Therapies
Tune Therapeutics	NC - Durham	Epigenetic modification to modulate gene expression
Tune Therapeutics	WA - Seattle	Epigenetic modification to modulate gene expression
Typewriter Therapeutics	MA - Cambridge	Gene Therapy
Tyris Therapeutics	Spain - Barcelona	Gene Therapies
Ultragenyx Pharmaceutical	CA - Brisbane	Small Molecules, Biologics
Ultragenyx Pharmaceutical	CA - Novato	Small Molecules, Biologics, Gene Therapy, mRNA, Antisense Oligo
Ultragenyx Pharmaceutical	MA - Bedford	Small Molecules, Biologics, Gene Therapy, mRNA, Antisense Oligo
Ultragenyx Pharmaceutical	MA - Somerville	Small Molecules, Biologics
Ultragenyx Pharmaceutical	MA - Woburn	Small Molecules, Biologics
uniQure	Netherlands - Amsterdam	Gene Therapy
Unnatural Products	CA - Santa Cruz	Macrocylic Peptides plus AI
Valerio Therapeutics	France - Paris	Orphan Diseases, Decoy Oligonucleotides
Valo Therapeutics	Finland - Helsinki	Oncolytic Virus, Peptide
Vaxxinity	TX - Dallas	Endobody Vaccines, Synthetic Peptides Vaccine
VectorY Therapeutics	Netherlands - Amsterdam	Vectorized Antibodies
Velvet Therapeutics	TX - Houston	Gene Therapies
VeonGen Therapeutics	Germany - Planegg	AAV Gene Therapy
Vernagen	GA - Tucker	mRNA Therapies
Verrica Pharmaceuticals	PA - West Chester	Topical therapies
Versameb	Switzerland - Basel	RNA Therapeutics
Verve Therapeutics	MA - Boston	Gene-editing Treatments
Vico Therapeutics	Netherlands - Leiden	Oligonucleotide based RNA modulating therapeutics
ViferaXS	Germany - Tübingen	Immunopeptidome-based antigen
Vigeo Therapeutics	MA - Cambridge	Biologics for Cancer
Vir Biotechnology	CA - San Francisco	Infectious disease therapies
Vir Biotechnology	Switzerland - Bellinzona	Infectious disease therapies
Vironexis Biotherapeutics	CA - San Diego	T Cell Immunotherapy
Virothera	UK - Cambridge	Gene Immunotherapeutics
Visirna Therapeutics	China - Shanghai	RNAi Therapeutics: siRNA Drugs
Vivet Therapeutics	France - Paris	Gene Therapy for Orphan Diseases
Voyager Therapeutics	MA - Lexington	AAV capsid Gene Therapy
WaVe Life Sciences	Japan - Kagoshima	Stereopure oligonucleotides
WaVe Life Sciences	MA - Cambridge	Stereopure oligonucleotides
Westlake Genetech	China - Hangzhou	AI-powered Gene Therapy Development
Xequel Bio	Virtual - Virtual	Peptide for Injury Healing
Xinnate	Sweden - Lund	Peptide-based Drugs
XyloCor Therapeutics	PA - King of Prussia	Gene Therapy
YouthBio Therapeutics	ON - Toronto	Gene therapies aimed at restoring more youthful epigenetic profiles with the help of partial reprogramming
Zata Pharmaceuticals	MA - Worcester	RNA, DNA Therapeutics
Zealand Pharma	Denmark - Soborg	Peptide Drugs
Ziphius Vaccines	Belgium - Merelbeke	Self-amplifying RNA Vaccine
Zucara Therapeutics	ON - Toronto	Peptide analog for diabetes treatment