524 Gene Therapy, RNA & Peptide Therapy Companies - Worldwide

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13therapeutics	OR - Portland	Peptide Therapeutics
4D Molecular Therapeutics	CA - Emeryville	Gene Therapy
A28 Therapeutics	CA - La Jolla	Targeted Lytic Peptides for the Treatment of Cancer
Aanastra	CA - Los Angeles	RNA therapeutics
AaviGen	Germany - Heidelberg	Precision gene therapies for heart failure
AAVogen	MD - Rockville	Gene therapeutics to strengthen muscle and fight disease
Abeona Therapeutics	OH - Cleveland	Therapies for Sanfilippo (SF) Syndrome Type A and Type B.
Abintus Bio	CA - San Diego	Gene Therapy
Abogen	China - Suzhou	mRNA
ADARx Pharmaceuticals	CA - San Diego	RNA Therapeutics
AddGraft Therapeutics	IL - Chicago	Gene Delivery Platform
Addimmune	MD - Rockville	HIV Gene Therapy
Adolore BioTherapeutics	FL - Delray Beach	Gene Therapy Analgesic for Pain
Adrenas Therapeutics	NC - Raleigh	Gene Therapy
Adverum Biotechnologies	CA - Redwood City	Adeno-Associated Virus Delivery, Gene Therapy
Aera Therapeutics	MA - Cambridge	Genetic Medicines
Affinia Therapeutics	MA - Waltham	Gene Delivery
Aileron Therapeutics	MA - Boston	Perpetually Active Peptides
Akouos	MA - Boston	Gene Therapy for Hearing Disorders
Alcyone Therapeutics	MA - Lowell	Gene Therapy
Aligos Therapeutics	CA - South SF	Therapies for hepatologic diseases and viral infections
Alivexis	Japan - Tokyo	Peptide Discovery?
Alltrna	MA - Cambridge	tRNA therapies
Allysta Pharmaceuticals	WA - Bellevue	Therapeutic Peptides
Alnylam Pharmaceuticals	MA - Cambridge	RNAi
Alnylam Pharmaceuticals	Switzerland - Zug	RNAi
Alnylam Pharmaceuticals	UK - Maidenhead	RNAi
Alpha-1 Biologics	NY - Stony Brook	Small molecules, peptides, diagnostic, vaccine
Altamira Therapeutics	DE - Newark	RNA Therapies
Altamira Therapeutics	Ireland - Dublin	RNA Therapies
Altamira Therapeutics	Switzerland - Basel	RNA Therapies
Altheia Science	Italy - Milan	Cell & Gene Therapy for Autoimmune Disorders
AltPep	WA - Seattle	Alternating Peptides for Neurological Diseases
AlveoGene	UK - Oxford	Inhaled Gene Therapy
Alzamend Neuro	CA - Newport Beach	Alzheimer's Treatment
Amarna Therapeutics	Netherlands - Leiden	Viral Gene Delivery Platform
Amaroq Therapeutics	New Zealand - Auckland	lncRNA Therapeutics
Ambulero	FL - Miami	Cell & Gene Therapies
American Gene Technologies	MD - Rockville	Gene Therapy and Immunotherapy Company. Lentiviral Vector Platform and Indication-Specific Technologies. Lead Therapeutics for an HIV Cure, Liver Cancer Cure, and PKU therapy
Ampersand Biomedicines	MA - Boston	AND-Body Therapeutics
Amplo Biotechnology	CA - San Diego	Treatment for congenital myasthenic syndromes
Amyndas Pharmaceuticals	Greece - Glyfada	Peptide for various disorders
Amytrx Therapeutics	AL - Birmingham	Peptide Therapies
Amytrx Therapeutics	TN - Nashville	Peptide Therapies
Anjarium Biosciences	Switzerland - Schlieren	Non-viral Gene Therapy
Antag Therapeutics	Denmark - Copenhagen	Therapeutic peptides for dietary-related metabolic diseases
Antion Biosciences	Switzerland - Plan-les-Ouates	Gene & Cell Therapy
Apellis Pharmaceuticals	Australia - Victoria	Cyclic peptide analog
Apellis Pharmaceuticals	CA - San Francisco	Cyclic peptide analog
Apellis Pharmaceuticals	Germany - München	Cyclic peptide analog
Apellis Pharmaceuticals	MA - Waltham	Cyclic peptide analog
Apellis Pharmaceuticals	Switzerland - Zug	Cyclic peptide analog
APEPTICO	Austria - Vienna	Peptide Drugs
Apertura Gene Therapy	NY - New York	AAV vectors for Gene Therapy
APIM Therapeutics	Norway - Rissa	Peptide Drugs
Aptadir	Italy - Milan	RNA Therapeutics
Aptahem	Sweden - Malmö	Aptamer-based Drugs
aptaTargets	Spain - Madrid	Aptamer Drugs
Arbutus Biopharma	PA - Warminster	RNAi
Arcturus Therapeutics	CA - San Diego	Lipid nanoparticle (LNP) mRNA drug delivery systems
Argo Biopharma	China - Shanghai	siRNA Drugs
Aro Biotherapeutics	PA - Philadelphia	Protein Scaffolds, Antisense Oligonucleotide
Arrowhead Pharmaceuticals	CA - Pasadena	RNAi
Arrowhead Pharmaceuticals	WI - Madison	RNAi
Art Bioscience	Israel - Rehovot	DMD Gene Therapy
Artery Therapeutics	CA - San Ramon	Peptide therapies
ARTHEx Biotech	Spain - Paterna	Antisense RNA Compounds
ARV Technologies	MD - North Bethesda	mRNA Vaccine Technology
Ascidian Therapeutics	MA - Boston	Mutated exon replacement
AsclepiX Therapeutics	MD - Bethesda	Peptide drugs
Aspa Therapeutics	CA - Palo Alto	Gene Therapy
Astellas	China - Shenyang	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	IL - Northbrook	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	Ireland - Dublin	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	Ireland - Killorglin	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	Japan - Takahagi	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	Japan - Tokyo	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	Japan - Yaizu	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Astellas	Netherlands - Meppel	Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies
Aston Sci.	Korea - Seoul	Therapeutic cancer vaccines and proteostasis modulators
Atalanta Therapeutics	MA - Boston	RNAi therapeutics
Atamyo Therapeutics	France - Evry	Gene Therapies targeting neuromuscular diseases
Atorvia Health Technologies	ON - Kanata	Kidney-targeted peptide that prevents regulated cell death and kidney failure
Atsena Therapeutics	NC - Durham	Gene Therapy
Attralus	CA - Burlingame	Amyloidosis Treatments
Avellino Laboratories	CA - Menlo Park	Gene Therapy, Molecular Diagnostics
AviadoBio	UK - London	Gene Therapies for neurodegenerative
Avidity Biosciences	CA - San Diego	Antibody-Oligonucleotide Conjugates
Avilex Pharma	Denmark - Copenhagen	Peptide for ischemic stroke
Avrion Therapeutics	Switzerland - Lausanne	Gene Therapies for Neurodegenerative Diseases
Avstera Therapeutics	PA - Malvern	Cell Therapy, Cancer Vaccine, mRNA
Axoltis Pharma	France - Lyon	Neurological Peptide Drugs
Axovia Therapeutics	UK - London	AAV Gene Therapy
Basking Biosciences	OH - Columbus	Reversible thrombolytic therapy for acute ischemic stroke
BDgene Therapeutics	China - Shanghai	mRNA-based CRISPR editing components
Beacon Therapeutics	MA - Cambridge	Gene Therapy
Beacon Therapeutics	UK - London	Gene Therapy
Bedrock Therapeutics	NC - Chapel Hill	AAV Research and Development Gene Therapy
Belief BioMed	China - Shanghai	AAV-delivered Gene Therapies
Benitec Biopharma	CA - Hayward	DdRNAi
Berlin Cures	Germany - Berlin	Aptamer for Cardio Indication
Bicycle Therapeutics	MA - Cambridge	Peptides
Bicycle Therapeutics	UK - Cambridge	Peptides
Bio-Path Holdings	TX - Bellaire	Antisense DNA therapeutics
Biojo Sciences	Korea - Seoul	Gene Therapy & Others
Biojo Sciences	MD - Bethesda	Gene Therapy & Others
BioNTech	CA - San Diego	mRNA, Vaccines, Biologics
BioNTech	Germany - Berlin	mRNA, Vaccines, Biologics
BioNTech	Germany - Idar-Oberstein	mRNA, Vaccines, Biologics
BioNTech	Germany - Mainz	mRNA, Vaccines, Biologics
BioNTech	MA - Cambridge	mRNA, Vaccines, Biologics
BioNTech	MD - Gaithersburg	mRNA, Vaccines, Biologics
Biorchestra	Korea - Daejeon	Novel RNA-based Therapeutics
Biorchestra	MA - Cambridge	Novel RNA-based Therapeutics
Biosortia Pharmaceuticals	OH - Dublin	Peptide Drugs
Biosyngen	Singapore - Singapore	Cell & Gene Therapy, Antibodies
BioViva Science	WA - Bainbridge Island	Gene Therapy Delivery
Black Swan Pharmaceuticals	NC - Wake Forest	Antisense RNA-based therapeutics for ALS
bluebird bio	MA - Somerville	Gene Therapy, Cellular Extraction & Reintroduction
Bolden Therapeutics	RI - Providence	Antisense Oligonucleotides for Neuro Indications
Borealis Biosciences	BC - Vancouver	RNA Medicien for Kidney Disease
BrightPath Biotherapeutics	Japan - Tokyo	Peptide Therapies
BRIM Biotechnology	Taiwan - Taipei	Peptides, Recombinant Proteins
Broken String Biosciences	UK - Cambridge	Gene Edited Cell & Gene Therapy
Capacity Bio	CA - Los Angeles	Mitophagy
Capsida Biotherapeutics	CA - Thousand Oaks	AAV Gene Therapy
Carbon Biosciences	MA - Waltham	Gene Therapy
Cardior Pharmaceuticals	Germany - Hanover	Non-coding RNA based therapeutics
Caregen Biopharma	Korea - Anyang	Growth Factors & Biomimetic Peptides
Carmine Therapeutics	Singapore - Singapore	Medicines based on red blood cell extracellular vesicles (RBCEVs), for the delivery of novel therapeutic modalities that include nucleic acids
Causeway Therapeutics	UK - Glasgow	microRNA
Cell BioEngines	NY - New York	Cell-based Immunotherapies
Cellastra	CA - San Francisco	Anti-scarring gene therapy/peptides
CellGenTech	Japan - Chiba	Ex-Vivo Gene Therapy
Ceria Therapeutics	AZ - Tucson	mRNA Delivery
Channavix Therapeutics	NY - Pittsford	Non-opioid analgesics
Chimerna Therapeutics	NY - New York	RNA Therapeutics
Chimeron Bio	PA - Philadelphia	Cancer Immunotherapy
Chondropeptix	Netherlands - Maastricht	Peptide for cartilage improvement
Chrysalis BioTherapeutics	TX - Galveston	Peptide to stimulate tissue regeneration
Cidara Therapeutics	CA - San Diego	Small molecules, peptide
Circle Pharma	CA - South SF	Macrocyclic Therapeutics
CircNova	MI - Detroit	Circular RNA
CiVi Biopharma	MD - Chevy Chase	Novel therapies against cardiometabolic diseases
CLAIRIgene	NC - Durham	Viral Vector Gene Therapy
Coave Therapeutics	France - Paris	Gene Therapy in Ophthalmology
Code Biotherapeutics	PA - Hatfield	DNA-based Gene Therapy Vector
Codone Biotechnology	China - Shanghai	tRNA Therapies
Coegin Pharma	Sweden - Lund	Inflammatory Targeting, Small Molecules & Peptides
CohBar	CA - Menlo Park	Mitochondrial-Derived Peptides
Comanche Biopharma	MA - Concord	siRNA for Preeclampsia
CombiGene	Sweden - Lidingö	Gene Therapy
Complement Therapeutics	UK - London	Complement Medicines - AAV Gene Therapy, Biologics
Constant Therapeutics	MA - Boston	Peptide Treatments
Courage Therapeutics	MA - Newton	Eating Disorder Treatments
Crane Biosciences	UK - London	Gene Therapies
Creyon Bio	CA - Carlsbad	Oligonucleotide-based Medicines
Curamys	Korea - Seoul	Stem Cell Fusion Technology

CureGenetics	China - Suzhou	Gene-editing - Diagnostics, Therapies
CureVac	Germany - Tübingen	MRNA treatments
CureVac	MA - Boston	MRNA treatments
CuroNZ	New Zealand - Hamilton	Neural Regeneration Peptides
Cytovation	Norway - Bergen	Peptide for cancer
Cytovation	UK - London	Peptide for cancer
Cyxone	Sweden - Malmö	Immunomodulating cyclotides for the treatment of autoimmune diseases
Deep Genomics	ON - Toronto	AI-discovery, Oligonucleotide Therapies
Diapin Therapeutics	MI - Ann Arbor	Peptide for diabetes
DIMERx	CA - San Francisco	Amino Acid Prodrug Dimer
DiNAQOR	CA - Laguna Hills	Gene Therapy for Heart Conditions
DiNAQOR	Germany - Hamburg	Gene Therapy for Heart Conditions
DiNAQOR	Switzerland - Schlieren	Gene Therapy for Heart Conditions
DNARx	CA - San Francisco	DNARx specializes in developing gene delivery technologies for cancer, heart disease, and neurodegenerative diseases including Alzheimer’s
Duet BioTherapeutics	CA - Pasadena	Bifunctional oligonucleotides for immuno-oncology
Dydo Pharma	Japan - Osaka	Small Molecules, Gene Therapy
Dynavax Technologies	CA - Emeryville	Synthetic oligonucleotides vaccines
EA Pharma	Japan - Tokyo	Amino Acid Treatments
EG 427	France - Paris	Pinpoint Gene Therapy
Eldec Pharmaceuticals	NC - Durham	Peptide Therapies
Eleven Therapeutics	Israel - Tel Aviv	Small interfering RNAs with ultra-long durability by utilizing high throughput combinatorial chemistry and AI
Eleven Therapeutics	UK - Cambridge	Small interfering RNAs with ultra-long durability by utilizing high throughput combinatorial chemistry and AI
Eli Lilly	CA - San Diego	Biologics Discovery
Eli Lilly	France - Neuilly-sur-Seine	Small Molecules, Biologics
Eli Lilly	IN - Indianapolis	Small Molecules, Biologics
Eli Lilly	Ireland - Kinsale	Small Molecules, Biologics
Eli Lilly	Italy - Sesto Fiorentino	Small Molecules, Biologics
Eli Lilly	MA - Cambridge	Small Molecules, Biologics
Eli Lilly	Mexico - San José	Small Molecules, Biologics
Eli Lilly	PR - Carolina	Recombinant Insulin
Eli Lilly	PR - Mayaguez	Small Molecules, Biologics
Eli Lilly	Spain - Alcobendas	Small Molecules, Biologics
Eli Lilly	UK - Basingstoke	Small Molecules, Biologics
Elicera Therapeutics	Sweden - Gothenburg	Cell & Gene Therapy Immuno-Oncology
Elpida Therapeutics	CA - Encino	Gene Therapy for Rare Disease
Emmaus Life Sciences	CA - Torrance	Oral amino acid treatment
Encoded Therapeutics	CA - South SF	Gene Therapy
Endsulin	WI - Madison	Genetic therapy for type 1 diabetes
Enterosys	France - Labege	Oral Peptides
Envoya	MA - Boston	Gene Therapy
EOM Pharmaceuticals	NJ - Montvale	Peptide-nucleic Acid Solutions
Epics Therapeutics	Belgium - Gosselies	RNA Therapies
EpilepsyGTx	UK - Waterbeach	Epilepsy Gene Therapy
Epsilon Molecular Engineering	Japan - Saitama	Heavy chain single domain antibodies
EsoBiotec	Belgium - Brabant Wallon	Cell & Gene Cancer Immunotherapies
Esperovax	MI - Plymouth	Targeted Oral mRNA
Esteve	Spain - Barcelona	Small Molecules, Gene Therapy
Ethris	Germany - Planegg	MRNA-based therapies, vaccines
ExCellThera	QC - Montréal	Growing blood stem cells for therapeutic use
ExcepGen	CA - San Francisco	RNA Therapeutics Platform
Excision BioTherapeutics	CA - San Francisco	Gene Editing
Exegenesis Bio	China - Hangzhou	Gene Therapy
Exegenesis Bio	MA - Lexington	Gene Therapy
Exegenesis Bio	PA - Lower Gwynedd	Gene Therapy
ExploRNA Therapeutics	Poland - Warsaw	mRNA Therapies
Expression Therapeutics	GA - Tucker	Gene Therapies
Exsilio Therapeutics	MA - Boston	Developing genomic medicines that insert therapeutic genes into safe harbors within the DNA
Feldan Therapeutics	QC - Quebec City	Peptide-based Intracellular Delivery Technology
Fennec Pharmaceuticals	NC - Durham	Small Molecules, Cyclic Peptides
Find Therapeutics	QC - Saint-Laurent	GPCR-Targeting Therapeutics
Flamingo Therapeutics	Belgium -	RNA Therapeutics
Flashpoint Therapeutics	IL - Chicago	Nanoscale design of therapeutic architecture to optimize anti-cancer immune response
Fractyl Health	MA - Lexington	Thermal ablation therapy, Gene Therapy
Frontera Therapeutics	China - Suzhou	Gene Therapy Development
Frontera Therapeutics	MA - Bedford	Gene Therapy Development
Gemvax & KAEL	Korea - Daejeon	Peptide Immunotherapy
Genascence	CA - Palo Alto	Musculoskeletal Gene Therapies
Gene Therapy Research Institute (GTRI)	Japan - Kanagawa	Gene Therapy
GenEdit	CA - South SF	Nonviral CRISPR-delivery system
Genenta Science	Italy - Milan	Gene Therapy
Geneos Therapeutics	PA - Philadelphia	Plasmid-based Neoantigen-targeted Cancer Therapies
Generation Bio	MA - Cambridge	Gene Therapy
Genervon Biopharmaceuticals	CA - Pasadena	Synthetic Peptide
Genespire	Italy - Milan	Gene Therapy
Généthon	France - Evry	Gene Therapy
GeneVentiv Therapeutics	NC - Raleigh	Gene Therapy
Genexine	Korea - Seoul	Biologics, DNA Plasmid Vaccine
Genflow Biosciences	Belgium - Charleroi	Anti-aging Gene Therapy
Genflow Biosciences	UK - London	Anti-aging Gene Therapy
GenKOre	Korea - Daejeon	Gene-editing therapies
GenKOre	Korea - Seoul	Gene-editing therapies
Genosera	OH - Columbus	Gene Therapy
Genprex	TX - Austin	Immunogene Therapy
GenSight Biologics	France - Paris	Ophthalmic Gene Therapy
GenVivo	CA - San Marino	Proprietary Gene Delivery Technology
GlioCure	France - Angers	Peptide
GQ Bio	Germany - Hamburg	Gene Therapy for Osteoarthritis
Grace Science	CA - Menlo Park	Therapies based on the function of NGLY1, AAV gene therapy, small molecules
Gradalis	TX - Carrollton	Cancer immunotherapy, RNAi
Gritgen Therapeutics	China - Suzhou	Gene Therapy
Guardian Therapeutics	MA - Lexington	Aptamer Therapeutics
Harness Therapeutics	UK - Cambridge	IncRNA
HAYA Therapeutics	CA - San Diego	RNA-based, RNA-targeting Fibrotic Therapies
HAYA Therapeutics	Switzerland - Lausanne	RNA-based, RNA-targeting Fibrotic Therapies
hC Bioscience	MA - Boston	tRNA-based Therapeutics
Helix Nanotechnologies	MA - Boston	DNA Therapy
Helixmith	Korea - Seoul	plasmid DNA based gene therapy
Hemera Biosciences	MA - Waltham	Gene Therapy
Heqet Therapeutics	Italy - Turin	Noncoding RNA as Therapeutic
Highlight Therapeutics	Spain - Valencia	Immuno-oncology, synthetic dsRNA complex
HitGen	China - Chengdu	DNA encoded library for drug discovery
Holostem Tarapie Avanzate	Italy - Modena	Cell & Gene Therapy
HuidaGene Therapeutics	China - Shanghai	Gene Therapy, Gene editing platform, delivery vector platform
Hunterian Medicine	MA - Cambridge	CRISPR-based drug discovery
Hybridize Therapeutics	Netherlands - Oegstgeest	RNA treatments for kidney disease
Ibex Biosciences	MD - Cumberland	Biologics, Cell Therapy, Gene Therapy
iCell Gene Therapeutics	NY - Stony Brook	Gene Therapy for Cancer
Ikarovec	UK - Norwich	Ocular Gene Therapy
ILC Therapeutics	UK - Lanarkshire	Synthetic Peptides
Immorna Biotherapeutics	China - Shanghai	Self-Replicating RNA
Immuno Cure Biotech	China - Hong Kong	Therapeutic Antibodies, DNA Vaccines
Impilo Therapeutics	CA - San Diego	ASOs
Imugene	Australia - Sydney	Peptide immunotherapy
InnoSkel	France - Biot	Therapies for Rare Skeletal Diseases
Innovac Therapeutics	MA - Cambridge	RNA Therapeutics
InnoVec Biotherapeutics	China - Beijing	AAV-Based Gene Therapy
Inomagen Therapeutics	IL - Chicago	Gene Therapies for Atrial Fibrillation
Inotrem	France - Paris	Peptide Therapy
Inotrem	France - Vandoeuvre	Peptide Therapy
Inovio Pharmaceuticals	CA - San Diego	DNA Vaccines
Inovio Pharmaceuticals	PA - Plymouth Meeting	DNA Vaccines
Inozyme Pharma	MA - Boston	Enzyme Replacement Therapy
Inspire Biotherapeutics	QC - Montréal	AAV Gene Therapy Platform
Interius BioTherapeutics	PA - Philadelphia	Novel methods for in vivo cell-specific gene delivery
InterK Peptide Therapeutics	Australia - Lane Cove West	Synthetic Peptides to Treat Cancer
Invectys	France - Paris	DNA Vaccine
invIOs	Austria - Vienna	Novel cancer immunotherapies, cell, siRNA, peptides
IO Biotech	Denmark - Copenhagen	Immuno-Oncology
Ionis Pharmaceuticals	CA - Carlsbad	RNA
Jaguar Gene Therapy	IL - Lake Forest	AAV-Based Gene Therapies
Jalon Therapeutics	France - Paris	Cell-Penetrating Peptide
Jaya Biosciences	CA - South SF	CNS-directed gene therapies
Jaya Biosciences	NC - Chapel Hill	CNS-directed gene therapies
Juniper Biologics	Singapore - Singapore	Small Molecules, Cell Therapy, Gene Therapy
Kailera Therapeutics	CA - San Diego	Peptides, Small Molecules
Kailera Therapeutics	MA - Waltham	Peptides, Small Molecules
Kairos Pharma	CA - Los Angeles	Cell Therapy, Antibodies, Small Molecules
Kate Therapeutics	CA - San Diego	AAV-based gene therapy for muscle disease
Kelonia Therapeutics	MA - Boston	in vivo CAR T Gene Therapy
Kinea Bio	WA - Seattle	Gene Therapy for Muscle Disease
Kither Biotech	Italy - Torino	Therapies for the treatment of rare pulmonary diseases
Kolon Life Science	Korea - Seoul	Cell & Gene Therapy, APIs
Korro Bio	MA - Cambridge	RNA-editing Drugs
Kriya Therapeutics	CA - Redwood City	Gene Therapy
Kriya Therapeutics	NC - Morrisville	Gene Therapy
Krystal Biotech	PA - Pittsburgh	Gene Therapy
Lactocore	MA - Newton	CNS Peptides
Lassogen	CA - San Diego	Lasso peptide-based therapies
Lateral Pharma	Australia - Melbourne	Repurposed Peptide
Leal Therapeutics	MA - Worcester	CNS Therapies
Lerna Biopharma	Singapore - Singapore	Nucleic Acid Therapeutics
Lexeo Therapeutics	NY - New York	Gene Therapy
Ligandal	NY - New York	Nanomedicine delivery for Genetic Medicines
Longevity Biotech	PA - Philadelphia	Synthetic Peptides
Luxna Biotech	Japan - Osaka	Oligonucleotide Therapeutics
Lytica Therapeutics	MA - Cambridge	Antimicrobial peptide Design
Lytix Biopharma	Norway - Oslo	Oncolytic Peptide
Mahzi Therapeutics	CA - San Mateo	Gene therapy for rare genetic neurodevelopmental disorders
MAIA Biotechnology	IL - Chicago	Peptide Cancer Therapies

Mammoth Biosciences	CA - Brisbane	CRISPR, Gene-Editing Therapies
Matice Biosciences	MA - Cambridge	Peptides for Scar Reduction
Matrix Biomed	CA - Irvine	Gene therapy for various cancers
Maze Therapeutics	CA - South SF	Small Molecules, Gene Therapy, Antisense Oligonucleotides, Biologics
MBX Biosciences	IN - Carmel	Hormone Analogues for Rare Endocrine Diseases
MDimune	Korea - Seoul	Drug Delivery Based on Cell-Derived Vesicles
Medera	MA - Boston	Cell & Gene Therapies
Medikine	CA - San Diego	Small Molecules, Peptide
MeiraGTx	UK - London	Gene Therapy
Merlin Biotech	PA - Doylestown	RNA Technology
Metsera	NY - New York	Obesity Therapies, Peptides, Antibodies
MimiVax	NY - Buffalo	Immunotherapeutics
MiNA Therapeutics	UK - London	Small activating RNA
miRecule	MD - Gaithersburg	microRNA Therapeutics for Cancer
Mitotherapeutix	CT - Farmington	siRNA drugs
Modalis Therapeutics	Japan - Tokyo	Genome Editing Tools for Therapeutic Discovery
Modalis Therapeutics	MA - Waltham	Genome Editing Tools for Therapeutic Discovery
Moderna Therapeutics	MA - Cambridge	RNA Therapies
Moderna Therapeutics	MA - Norwood	RNA Therapies
Momotaro-Gene	Japan - Okayama	Cancer Gene Therapy
Mustang Bio	MA - Worcester	Immunotherapies
MyoPax	Germany - Berlin	Cell & Gene Therapies
Myosana Therapeutics	WA - Seattle	Non-viral Gene Therapy
Myrtelle	MA - Wakefield	Gene Therapy
NanoCell Therapeutics	PA - Wayne	Gene Therapy
Nanogenics	UK - Selkirk	Gene Therapy
Nanoscope Therapeutics	TX - Dallas	AAV-delivered opsin
NapaJen Pharma	Japan - Tokyo	Oligonucleotide Drugs
NapaJen Pharma	WA - Seattle	Oligonucleotide Drugs
Navega Therapeutics	CA - San Diego	Chronic Pain Treatment
NeoMatrix Therapeutics	NY - Stony Brook	Bioactive Peptides for Burn Healing
Nephrogen	NY - New York	Gene Therapy for Kidney Disease
NervGen Pharma	BC - Vancouver	Peptide inhibitor of protein tyrosine phosphatase sigma
NeuExcell Therapeutics	PA - Philadelphia	Gene Therapy for Neural Regeneration & Repair
Neurexis Therapeutics	CO - Aurora	Peptide for Cardiac Indications
Neurogene	NY - New York	Genetic Therapies
Neurogene	TX - Houston	Genetic Therapies
Neurophth Therapeutics	China - Wuhan	Ophthalmology Gene Therapy
NeuroQure	CA - Coto de Caza	Gene Therapy for Neurological Disorders
Neuroscientific Biopharmaceuticals	Australia - Cottesloe	Peptide for neurological treatments
Neurotez	NJ - Bridgewater	Peptide Treatment for Alzheimer's
NeuShen Therapeutics	China - Shanghai	AAV Gene Therapy, Small Molecules
Nimble Therapeutics	WI - Madison	Photoprotected Amino Acids
Nitto BioPharma	CA - San Diego	Drug Delivery of siRNA
Nosopharm	France - Lyon	Anti-infectives, Peptide
Novartis	CA - San Diego	Small Molecules, Vaccines, Biologics
Novartis	MA - Cambridge	Small Molecules, Vaccines, Biologics / Diagnostics
Novartis	Mexico - Mexico City	Small Molecules, Vaccines, Biologics
Novartis	NJ - East Hanover	Small Molecules, Vaccines, Biologics
Novartis	Switzerland - Basel	Small Molecules, Vaccines, Biologics
Nuevocor	Singapore - Singapore	AAV-based gene therapy
Nuntius Therapeutics	UK - London	mRNA Therapies
Nuravax	CA - Irvine	DNA Vaccine
Nykode Therapeutics	Norway - Oslo	Therapeutic DNA Vaccine
NysnoBio	CA - Mill Valley	Parkin protein therapeutics
Obsidian Therapeutics	MA - Cambridge	Cell & Gene Therapies
Ocelot Bio	CA - Redwood City	Peptide therapeutic to treat complications of end-stage liver disease
Ochre Bio	UK - Oxford	siRNA liver drugs
Oculogenex	CA - La Habra	Gene Therapy for Vision
Odimma Therapeutics	France - Strasbourg	Personalized Cancer Immunotherapy
OliPass	Korea - Gyeonggi	Peptide nucleic acid derivatives
OliX Pharmaceuticals	Korea - Gyeonggi	RNAi Treatments
Omega Therapeutics	MA - Cambridge	Gene Editing
Oncogenuity	FL - Bay Harbor Islands	Oligonucleotide platform for the treatment of genetically driven cancers
Oncolyze	NY - New York	Peptide Therapy
OncoSenX	WA - Seattle	Proteo-Lipid Vehicle (PLV) and plasmid DNA for cancer
Oncotherapy Science	Japan - Kawasaki	Small Molecule, peptides, antibody therapies, contract analytical
Oncovir	DC - Washington	dsRNA viral mimic
ONL Therapeutics	MI - Ann Arbor	Small molecule peptide
Opus Genetics	NC - Durham	Ophthalmology Gene Therapy
Orbital Therapeutics	MA - Cambridge	RNA technology (not RNAi)
Orchard Therapeutics	MA - Boston	Ex-vivo autologous hematopoietic stem cell gene therapy
Orchard Therapeutics	UK - London	Ex-vivo autologous hematopoietic stem cell gene therapy
Orna Therapeutics	MA - Watertown	oRNA, Delivery
Orphion Therapeutics	NY - New York	Gene Therapy
OrthoTrophix	CA - Oakland	Bone, cartilage and teeth therapies
Oryn Therapeutics	CA - Redwood City	Macrocyclic peptide therapeutics
Oryx Translational Medicine	Germany - Vaterstetten	Cancer Immunotherapy
Otovia Therapeutics	China - Shanghai	Drugs for Inner Ear Hearing Loss
Ovoca Bio	Ireland - Dublin	Nasally Delivered Synthetic Peptide
Oxalo Therapeutics	IL - Chicago	Peptide-based therapeutics to treat rare renal diseases and prevent recurrent kidney stones
Oxular	UK - Oxford	Gene Therapy
Pantherna Therapeutics	Germany - Hennigsdorf	Nanoparticle Delivery for mRNA drugs
Passage Bio	PA - Philadelphia	Gene Therapy
PCI Biotech	Norway - Oslo	Drug Delivery
PEEL Therapeutics	UT - Salt Lake City	Nature-inspired Cancer Therapies
PEP-Therapy	France - Paris	Peptide Therapies
Peptide Logic	CA - San Diego	Peptide-Antibody Conjugates
Peptilogics	PA - Pittsburgh	Peptide Therapeutics
Peptomyc	Spain - Barcelona	Cell Penetrating Peptides
Peptron	Korea - Daejeon	Peptide-based Medicine Platform
Peroxitech	PA - Philadelphia	Peptide treatment for acute lung injury
Perpetual Medicines	-	Computational peptide therapeutics
Pfizer	CA - La Jolla	Peptides, Monoclonal Antibodies
Pfizer	NC - Durham	Small Molecules, Vaccines, Biologics
PhageNova Bio	NJ - Summit	Gene Delivery Vector
Phaim Pharma	UK - London	Peptide Diabetes Treatment
PharmaIN	WA - Bothell	Subcutaneous peptides, Out licensing
Phio Pharmaceuticals	MA - Marlborough	RNAi
Phlox Therapeutics	Netherlands - Naarden	Gene Therapy for Heart Disease
Phoenix Nest	NY - Brooklyn	Sanfilippo syndrome treatment
PinotBio	Korea - Suwon	Small molecules, ADC, Nucleoside-based Therapy
Plasticell	UK - Stevenage	Cell, Gene Therapy, Blood Products
Poolbeg Pharma	UK - London	Developing drugs to sell off
Poseida Therapeutics	CA - San Diego	Genome Editing Technologies
Precigen	MD - Germantown	Cell & Gene Therapy
Prevail Therapeutics	NY - New York	AAV-based gene therapies
Primera Therapeutics	MD - Rockville	mtDNA engineering toolbox for mitochondrial diseases
Prolifagen Therapeutics	PA - Villanova	microRNA
ProQR Therapeutics	MA - Cambridge	Oligonucleotide Therapy
ProQR Therapeutics	Netherlands - Leiden	Oligonucleotide Therapy
Protagenic Therapeutics	NY - New York	Neuro-Active Peptides
Protagonist Therapeutics	Australia - Brisbane	Oral peptides
Protagonist Therapeutics	CA - Newark	Oral peptides for GI indications
ProtoKinetix	OH - Dalton	Anti-aging Glycopeptide
Providence Therapeutics	AB - Calgary	mRNA Cancer Vaccines
PulseSight Therapeutics	France - Paris	Ophthalmic Treatment Plasmid
Purespring Therapeutics	UK - London	Gene Therapy for Kidney Disease
PURMX Therapeutics	Japan - Hiroshima	Nucleic Acid Drugs
PYC Therapeutics	Australia - Nedlands	Peptide drug discovery
PYC Therapeutics	CA - Carlsbad	Peptide drug discovery
Ractigen Therapeutics	China - Nantong	Small activating RNA
Radar Therapeutics	-	Smart Programmable Medicines Using Molecular RNA Sensors
RainBIO	NC - Raleigh	Cornea Gene Therapy
Rampart Bioscience	CA - Monrovia	Non-viral, durable gene therapy
Ray Therapeutics	CA - San Francisco	Optogenetic Gene Therapy
ReAlta Life Sciences	VA - Norfolk	Complement and Inflammation Inhibition drug products
Recbio Technology	China - Taizhou	mRNA Covid Vaccine
ReCode Therapeutics	CA - Menlo Park	Nucleic Acid Therapeutic Delivery
Redbiotec	Switzerland - Schlieren	Various Biologic Modalities
Regel Therapeutics	CA - Berkeley	AAV gene delivery
Regel Therapeutics	MA - Cambridge	AAV gene delivery
RegeneRx Biopharmaceuticals	MD - Rockville	Peptides
ReGenTree	NJ - Princeton	Therapeutic Peptides
ReGenX Biosciences	MD - Rockville	Gene Therapy, Biologics
Regulus Therapeutics	CA - San Diego	MicroRNAs
Rejuvenate Bio	CA - San Diego	Gene Therapy for Aging
Rejuvenate Biomed	Belgium - Diepenbeek	Combination Drugs for Aging
Rejuvenation Technologies	CA - Mountain View	Telomere Extension via Nucleoside-modified TERT mRNA
Relief Therapeutics	Switzerland - Geneva	Peptide & Protein Therapies
Remedium Bio	MA - Needham	Gene Therapy
Renbio	NY - Long Island City	Gene Therapy Directing Antibody Creation in vivo
Renova Therapeutics	CA - Carlsbad	Gene Therapies
Repertoire Immune Medicines	MA - Cambridge	Cell & Peptide-Based Therapies
Replay	CA - San Diego	HSV Vector Gene Therapies
Replicate Bioscience	CA - San Diego	Preventing oncology drug resistance
Replicor	QC - Montréal	DNA, polymer, small molecule combination Hepatitis B treatment
ResoTher Pharma	Denmark - Holte	Cardiovascular Treatment
ResQ Biotech	Greece - Patra	Therapies for Protein Misfolding Diseases
Restore Vision	Japan - Tokyo	Gene Therapy for Blindness due to Retinal Disorders
Retromer Therapeutics	NY - New York	Retromer Enhancement via Macrocyclic Peptides
RheumaGen	CO - Denver	Cell & Gene Therapy
Rhythm Pharmaceuticals	MA - Boston	Peptide Therapeutics
Ribomic	Japan - Tokyo	Aptamers
RIGImmune	CT - Farmington	RNA Immunotherapeutics
Riptide Bioscience	CA - Vallejo	Peptide Therapeutics
Rithim Biologics	MD - Woodbine	Gene Therapy for Tachycardias
RNAimmune	MD - Germantown	mRNA therapies
Rocket Pharmaceuticals	NJ - Cranbury	Gene Therapies

Rona Therapeutics	China - Shanghai	RNA Therapeutics Platform
RosVivo Therapeutics	NV - Reno	miRNA & siRNA Therapies
Sagittarius Bio	CA - Thousand Oaks	Gene Therapy for Cancer
SalioGen Therapeutics	MA - Lexington	Gene Therapy Platform Technology
San Rocco Therapeutics	FL - Tampa	Gene Therapy, Orphan Diseases
Sana Biotechnology	WA - Seattle	Cell & Gene Therapies
SanegeneBio	MA - Woburn	siRNA Drug Discovery
Sapience Therapeutics	NY - Tarrytown	Peptide-based Therapies for cancers
Sapu BioScience	CA - San Diego	RNA & Small Molecule Immuno-oncology Therapies
Sciwind Biosciences	China - Hangzhou	Oral peptide delivery
Scopus BioPharma	NY - New York	Immuno-oncology Gene Therapy
Secarna Pharmaceuticals	Germany - Planegg	Antisense Oligonucleotide Therapies
Senisca	UK - Exeter	Antisense Oligonucleotides for Senescence
Senti Biosciences	CA - South SF	Gene Circuits; Cell & Gene Therapies
Sentia Medical Sciences	CA - San Diego	Novel peptide therapeutics
Seragon Biosciences	CA - Irvine	Small Molecules, Gene Therapy
Serodus	Norway - Oslo	Drug Development
Serpin Pharma	VA - Manassas	Peptide drugs
Shape Therapeutics	WA - Seattle	RNA-editing gene therapy
Shenogen Pharma	China - Beijing	Small Molecules, Biologics, Viral
Silence Therapeutics	Germany - Berlin	RNAi
Silence Therapeutics	NJ - Hoboken	RNAi
Silence Therapeutics	UK - London	RNAi
Sinfonia Biotherapeutics	RI - Warren	Nervous System Therapies
Sinfonia Biotherapeutics	Sweden - Huddinge	Nervous System Therapies
Siren Biotechnology	CA - San Francisco	AAV Immuno-Gene Therapy
Sirius Therapeutics	CA - San Diego	RNAi Therapies
Sirius Therapeutics	China - Shanghai	RNAi Therapies
siRNAgen	Korea - ZZ	siRNA Therapeutics
Sirnaomics	China - Suzhou	RNAi Therapeutics
Sirnaomics	MD - Germantown	RNAi Therapeutics
Sisaf	UK - Guildford	RNA Therapies for Rare Diseases
Skip Therapeutics	Israel - Ness Ziona	RNA-based therapies for rare genetic disorders and common diseases
Skylark Bio	MA - Cambridge	Gene Therapy for Hearing Disorders
Skyline Therapeutics	China - Shanghai	AAV Gene Therapy
SmartPharm Therapeutics	MA - Cambridge	Production of biologics within patients via gene therapy
SNIPR BIOME	Denmark - Copenhagen	CRISPR for microbiome management, genetically-modified bacteriophages
SOLA Biosciences	MA - Natick	Gene Therapies for Protein Misfolding Diseases
Solid Biosciences	MA - Charlestown	Gene Therapy, Devices, Biologics, Small Molecules all for DMD
Sonata Therapeutics	MA - Watertown	Small Molecules, Gene Therapy
SonoThera	CA - South SF	Ultrasound-Guided Gene Therapy
Soricimed Biopharma	NB - Moncton	Proprietary TRPV6-targeting peptide platform
SparingVision	France - Paris	Retinal Gene Therapy Treatments
SparingVision	PA - Philadelphia	Retinal Gene Therapy Treatments
Spark Therapeutics	PA - Philadelphia	Singe Dose Gene Therapy
Spine BioPharma	NY - New York	Amino acid peptide for spinal pain relief
Spirovant Sciences	PA - Philadelphia	Gene Therapy - Lung Diseases
Splash Pharmaceuticals	CA - San Diego	Peptide
SpliceBio	Spain - Barcelona	Intein Technologies - Gene Therapy
SpliSense	Israel - Jerusalem	Antisense Oligonucleotides
Spotlight Therapeutics	CA - Hayward	In vivo Gene Editing
Spur Therapeutics	UK - Stevenage	Protein replacement via Gene Therapy
Starna Therapeutics	China - Suzhou	mRNA vaccine, therapies
StemCardia	CA - Sacramento	Cell & gene therapies engineered to repair the heart
Sterna Biologicals & KG	Germany - Marburg	Antisense Molecule - DNAzyme
Stoke Therapeutics	MA - Bedford	Antisense Oligonucleotide Medicines
Strand Therapeutics	MA - Boston	Gene Therapy
StrideBio	NC - Durham	Antibody-Evading Gene Therapy
STRM.BIO	MA - Cambridge	Extracellular vesicles (EVs) to deliver gene therapies
Stylus Medicine	MA - Cambridge	Enzymatic Gene Therapy
Susavion Biosciences	AZ - Tempe	Bio-active Peptides
Suzhou Ribo Life Science Company	China - Kunshan	RNAi
Switch Therapeutics	CA - South SF	RNAi Therapies
Sylentis	Spain - Madrid	RNAi Treatments
SynerK	MA - Concord	RNA-targeted Therapies
SYNG Pharmaceuticals	ON - Kingston	Diagnostic, Peptide-based Non-Hormonal Treatment for Endometriosis
SYTE.bio	MA - Boston	Precision therapeutics using its proprietary Linear DNA and Circular RNA technology platforms
TAGCyx Biotechnologies	Japan - Tokyo	Oligonucleotide Drug Discovery Platform
Takara Bio	Japan - Shiga	Gene Therapy, Agribiotech, Biotech Lab Technology
Taysha Gene Therapies	TX - Dallas	Adeno-associated virus gene therapies
Temple Therapeutics	Netherlands - Geleen	Amino Acid-based Surgical Treatment
Tenaya Therapeutics	CA - South SF	Cardiovascular Therapeutics
Tern Therapeutics	DC - Washington	Gene Therapy for Batten Disease
Tevard Biosciences	MA - Cambridge	tRNA-based Gene Therapies
Theragene Pharmaceuticals	CA - San Diego	Immunotherapy, gene therapy and peptide delivery
Therorna	China - Beijing	RNA Therapies
TME Therapeutics	Japan - Tokyo	dsRNA Treatment for Cancer
Torque Bio	NC - Durham	Gene Therapies
TransCode Therapeutics	MA - Newton	RNA Delivery, Small Molecule
Transgene	France - Illkirch-Graffenstaden	Viral Vector Therapeutics, Gene Therapy
Transgene	France - Lyon	Viral Vector Therapeutics, Gene Therapy
Transgene	MA - Boston	Viral Vector Therapeutics, Gene Therapy
Treeway	Netherlands - Tilburg	Small Molecules, Gene Therapy
TuHURA Biosciences	FL - Tampa	Cancer Therapies
Tune Therapeutics	NC - Durham	Epigenetic modification to modulate gene expression
Tune Therapeutics	WA - Seattle	Epigenetic modification to modulate gene expression
Turn Biotechnologies	CA - Mountain View	mRNA Therapies
Tyris Therapeutics	Spain - Barcelona	Gene Therapies
Ultimovacs	Norway - Oslo	Immunotherapy
Ultragenyx Pharmaceutical	CA - Brisbane	Small Molecules, Biologics
Ultragenyx Pharmaceutical	CA - Novato	Small Molecules, Biologics, Gene Therapy, mRNA, Antisense Oligo
Ultragenyx Pharmaceutical	MA - Cambridge	Small Molecules, Biologics
Ultragenyx Pharmaceutical	MA - Somerville	Small Molecules, Biologics
Ultragenyx Pharmaceutical	MA - Woburn	Small Molecules, Biologics
uniQure	Netherlands - Amsterdam	Gene Therapy
Unnatural Products	CA - Santa Cruz	Macrocylic Peptides plus AI
Valerio Therapeutics	France - Paris	Orphan Diseases, Decoy Oligonucleotides
Valo Therapeutics	Finland - Helsinki	Oncolytic Virus, Peptide
Vault Pharma	CA - Los Angeles	Peptide payloads for immune signaling
Vaxxinity	TX - Dallas	Endobody Vaccines, Synthetic Peptides Vaccine
VectorY	Netherlands - Amsterdam	Vectorized Antibodies
Velvet Therapeutics	TX - Houston	Gene Therapies
Vernagen	GA - Tucker	mRNA Therapies
Verrica Pharmaceuticals	PA - West Chester	Topical therapies
Versameb	Switzerland - Basel	RNA Therapeutics
Verve Therapeutics	MA - Boston	Gene-editing Treatments
Vico Therapeutics	Netherlands - Leiden	Oligonucleotide based RNA modulating therapeutics
ViGeneron	Germany - Planegg	AAV Gene Therapy
Vigeo Therapeutics	MA - Cambridge	Biologics for Cancer
Vir Biotechnology	CA - San Francisco	Infectious disease therapies
Vir Biotechnology	MO - St. Louis	Infectious disease therapies
Vir Biotechnology	OR - Portland	Infectious disease therapies
Vir Biotechnology	Switzerland - Bellinzona	Infectious disease therapies
Viramatix Biotechnology	Malaysia - Kajang	Peptide based anti-viral therapeutics
Viramatix Biotechnology	UK - London	Peptide based anti-viral therapeutics
Viridian Therapeutics	CO - Boulder	MicroRNA
Viridian Therapeutics	MA - Waltham	MicroRNA
Vironexis Biotherapeutics	CA - San Diego	T Cell Immunotherapy
Virothera	UK - Cambridge	Gene Immunotherapeutics
Visgenx	CA - Santa Cruz	Therapeutics for Macular Degeneration and Other Age-Related Disorders
Vivet Therapeutics	France - Paris	Gene Therapy for Orphan Diseases
Voyager Therapeutics	MA - Lexington	AAV capsid Gene Therapy
WaVe Life Sciences	Japan - Kagoshima	Stereopure oligonucleotides
WaVe Life Sciences	MA - Cambridge	Stereopure oligonucleotides
Windtree Therapeutics	PA - Warrington	Peptides
WntResearch	Sweden - Lund	Peptide Therapies
Xequel Bio	SC - Mount Pleasant	Peptide for Injury Healing
Xequel Bio	TX - Fort Worth	Peptide for Injury Healing
Xinnate	Sweden - Lund	Peptide-based Drugs
XyloCor Therapeutics	PA - Wayne	Gene Therapy
YouthBio Therapeutics	ON - Toronto	Gene therapies aimed at restoring more youthful epigenetic profiles with the help of partial reprogramming
Zata Pharmaceuticals	MA - Worcester	RNA, DNA Therapeutics
Zealand Pharma	Denmark - Soborg	Peptide Drugs
Ziphius Vaccines	Belgium - Merelbeke	Self-amplifying RNA Vaccine
Zucara Therapeutics	ON - Toronto	Peptide analog for diabetes treatment