| 4D Molecular Therapeutics |
Emeryville, CA |
Gene Therapy |
| Abeona Therapeutics |
Cleveland, OH |
Therapies for Sanfilippo (SF) Syndrome Type A and Type B. |
| Abogen |
Suzhou, China |
mRNA |
| ADARx Pharmaceuticals |
San Diego, CA |
RNA Therapeutics |
| Addimmune |
Rockville, MD |
HIV Gene Therapy |
| Adverum Biotechnologies |
Redwood City, CA |
Adeno-Associated Virus Delivery, Gene Therapy |
| Affinia Therapeutics |
Waltham, MA |
Gene Delivery |
| Alcyone Therapeutics |
Lowell, MA |
Gene Therapy |
| Aligos Therapeutics |
South SF, CA |
Therapies for hepatologic diseases and viral infections |
| Alltrna |
Cambridge, MA |
tRNA therapies |
| Alnylam Pharmaceuticals |
Cambridge, MA |
RNAi |
| Alnylam Pharmaceuticals |
Zug, Switzerland |
RNAi |
| Alnylam Pharmaceuticals |
Maidenhead, UK |
RNAi |
| AltPep |
Seattle, WA |
Alternating Peptides for Neurological Diseases |
| Alzamend Neuro |
Atlanta, GA |
Alzheimer's Treatment |
| Amarna Therapeutics |
Leiden, Netherlands |
Viral Gene Delivery Platform |
| American Gene Technologies |
Rockville, MD |
Gene Therapy and Immunotherapy Company. Lentiviral Vector Platform and Indication-Specific Technologies. Lead Therapeutics for an HIV Cure, Liver Cancer Cure, and PKU therapy |
| Ampersand Biomedicines |
Boston, MA |
AND-Body Therapeutics |
| Antion Biosciences |
Plan-les-Ouates, Switzerland |
Gene & Cell Therapy |
| Apellis Pharmaceuticals |
Hawthorn East, Australia |
Cyclic peptide analog |
| Apellis Pharmaceuticals |
San Francisco, CA |
Cyclic peptide analog |
| Apellis Pharmaceuticals |
Munich, Germany |
Cyclic peptide analog |
| Apellis Pharmaceuticals |
Waltham, MA |
Cyclic peptide analog |
| Apellis Pharmaceuticals |
Zug, Switzerland |
Cyclic peptide analog |
| Arbutus Biopharma |
Warminster, PA |
RNAi |
| Arcturus Therapeutics |
San Diego, CA |
Lipid nanoparticle (LNP) mRNA drug delivery systems |
| Argo Biopharma |
Shanghai, China |
siRNA Drugs |
| Aro Biotherapeutics |
Philadelphia, PA |
Protein Scaffolds, Antisense Oligonucleotide |
| Arrowhead Pharmaceuticals |
Pasadena, CA |
RNAi |
| Arrowhead Pharmaceuticals |
San Diego, CA |
RNAi |
| Arrowhead Pharmaceuticals |
Madison, WI |
RNAi |
| Arrowhead Pharmaceuticals |
Verona, WI |
RNAi |
| Art Bioscience |
Rehovot , Israel |
DMD Gene Therapy |
| Ascidian Therapeutics |
Boston, MA |
Mutated exon replacement |
| Astellas |
Shenyang, China |
Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies |
| Astellas |
Northbrook, IL |
Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies |
| Astellas |
Dublin, Ireland |
Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies |
| Astellas |
Killorglin, Ireland |
Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies |
| Astellas |
Takahagi, Japan |
Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies |
| Astellas |
Tokyo, Japan |
Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies |
| Astellas |
Yaizu, Japan |
Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies |
| Astellas |
Meppel, Netherlands |
Small Molecules, ADC, Cell Therapy, Gene Therapy, Viral, Antibodies |
| Aston Sci. |
Seoul, Korea |
Therapeutic cancer vaccines and proteostasis modulators |
| Atalanta Therapeutics |
Boston, MA |
RNAi therapeutics |
| Atsena Therapeutics |
Durham, NC |
Gene Therapy |
| Attralus |
Naples, FL |
Amyloidosis Treatments |
| Avellino Laboratories |
Menlo Park, CA |
Gene Therapy, Molecular Diagnostics |
| Averna Therapeutics |
Ness Ziona, Israel |
Developing genomic medicines that insert therapeutic genes into safe harbors within the DNA |
| Averna Therapeutics |
Watertown, MA |
Developing genomic medicines that insert therapeutic genes into safe harbors within the DNA |
| AviadoBio |
London, UK |
Gene Therapies for neurodegenerative |
| Avidity Biosciences |
San Diego, CA |
Antibody-Oligonucleotide Conjugates |
| Avista Therapeutics |
Pittsburgh, PA |
Gene Therapy Delivery |
| Axoltis Pharma |
Lyon, France |
Neurological Peptide Drugs |
| Belief BioMed |
Shanghai, China |
AAV-delivered Gene Therapies |
| Bicycle Therapeutics |
Cambridge, MA |
Peptides |
| Bicycle Therapeutics |
Cambridge, UK |
Peptides |
| Bio-Path Holdings |
Bellaire, TX |
Antisense DNA therapeutics |
| Biojo Sciences |
Seoul, Korea |
Gene Therapy & Others |
| Biojo Sciences |
Bethesda, MD |
Gene Therapy & Others |
| Biomonadic |
Berkeley, CA |
Klotho Gene Therapy |
| BioNTech |
San Diego, CA |
mRNA, Vaccines, Biologics |
| BioNTech |
Berlin, Germany |
mRNA, Vaccines, Biologics |
| BioNTech |
Idar-Oberstein, Germany |
mRNA, Vaccines, Biologics |
| BioNTech |
Mainz, Germany |
mRNA, Vaccines, Biologics |
| BioNTech |
Cambridge, MA |
mRNA, Vaccines, Biologics |
| BioNTech |
Gaithersburg , MD |
mRNA, Vaccines, Biologics |
| Biorchestra |
Daejeon, Korea |
Novel RNA-based Therapeutics |
| Biorchestra |
Cambridge, MA |
Novel RNA-based Therapeutics |
| Biosyngen |
Singapore, Singapore |
Cell & Gene Therapy, Antibodies |
| Brink Therapeutics |
Paris, France |
Programmable recombinases |
| BRL Medicine |
Shanghai, China |
Cell & Gene Therapy Platforms |
| Broken String Biosciences |
Cambridge, UK |
Gene Edited Cell & Gene Therapy |
| Capsida Biotherapeutics |
Thousand Oaks, CA |
AAV Gene Therapy |
| Carbon Biosciences |
Waltham, MA |
Gene Therapy |
| Cardior Pharmaceuticals |
Hanover, Germany |
Non-coding RNA based therapeutics |
| Carmine Therapeutics |
Singapore, Singapore |
Medicines based on red blood cell extracellular vesicles (RBCEVs), for the delivery of novel therapeutic modalities that include nucleic acids |
| Causeway Therapeutics |
Glasgow, UK |
microRNA |
| Cell BioEngines |
New York, NY |
Cell-based Immunotherapies |
| Chimeron Bio |
Philadelphia, PA |
Cancer Immunotherapy |
| Cidara Therapeutics |
San Diego, CA |
Small molecules, peptide |
| CirCode Biomed |
Shanghai, China |
RNA Therapeutics |
| CLOVERNA |
Okayama, Japan |
RNA Targeting Oligonucleotides |
| Coave Therapeutics |
Paris, France |
Gene Therapy in Ophthalmology |
| Code Biotherapeutics |
Hatfield, PA |
DNA-based Gene Therapy Vector |
| Concinnity Genetics |
Glasgow, UK |
RNA-control of gene therapies |
| CureGenetics |
Suzhou, China |
Gene-editing - Diagnostics, Therapies |
| Deep Genomics |
Toronto, ON |
AI-discovery, Oligonucleotide Therapies |
| DiNAQOR |
Laguna Hills, CA |
Gene Therapy for Heart Conditions |
| DiNAQOR |
Hamburg, Germany |
Gene Therapy for Heart Conditions |
| DiNAQOR |
Schlieren, Switzerland |
Gene Therapy for Heart Conditions |
| Dogodan Therapeutics |
Westford, MA |
Nucleic Acid Therapeutics |
| Dynavax Technologies |
Emeryville, CA |
Synthetic oligonucleotides vaccines, adjuvants |
| EG 427 |
Paris, France |
Pinpoint Gene Therapy |
| Eleven Therapeutics |
Tel Aviv, Israel |
Small interfering RNAs with ultra-long durability by utilizing high throughput combinatorial chemistry and AI |
| Eleven Therapeutics |
Cambridge, UK |
Small interfering RNAs with ultra-long durability by utilizing high throughput combinatorial chemistry and AI |
| Eli Lilly |
San Diego, CA |
Biologics Discovery |
| Eli Lilly |
Neuilly-sur-Seine, France |
Small Molecules, Biologics |
| Eli Lilly |
Indianapolis, IN |
Small Molecules, Biologics |
| Eli Lilly |
Kinsale, Ireland |
Small Molecules, Biologics |
| Eli Lilly |
Sesto Fiorentino, Italy |
Small Molecules, Biologics |
| Eli Lilly |
Boston, MA |
Small Molecules, Biologics |
| Eli Lilly |
San José, Mexico |
Small Molecules, Biologics |
| Eli Lilly |
Carolina, PR |
Recombinant Insulin |
| Eli Lilly |
Mayaguez, PR |
Small Molecules, Biologics |
| Eli Lilly |
Alcobendas, Spain |
Small Molecules, Biologics |
| Eli Lilly |
Basingstoke, UK |
Small Molecules, Biologics |
| Emmaus Life Sciences |
Torrance, CA |
Oral amino acid treatment |
| Encoded Therapeutics |
South SF, CA |
Gene Therapy |
| Endsulin |
Madison, WI |
Genetic therapy for type 1 diabetes |
| Engage Bio |
San Carlos, CA |
Tethosome Gene Therapy |
| Epics Therapeutics |
Gosselies, Belgium |
RNA Therapies |
| Epsilon Molecular Engineering |
Saitama, Japan |
Heavy chain single domain antibodies |
| Esteve |
Barcelona, Spain |
Small Molecules, Gene Therapy |
| Ethris |
Planegg, Germany |
MRNA-based therapies, vaccines |
| ExCellThera |
Montréal, QC |
Growing blood stem cells for therapeutic use |
| ExcepGen |
San Francisco, CA |
RNA Therapeutics Platform |
| Excision BioTherapeutics |
San Francisco, CA |
Gene Editing |
| Exegenesis Bio |
Hangzhou, China |
Gene Therapy |
| Exegenesis Bio |
Lexington, MA |
Gene Therapy |
| Exegenesis Bio |
Horsham, PA |
Gene Therapy |
| Feldan Therapeutics |
Quebec City, QC |
Peptide-based Intracellular Delivery Technology |
| Fennec Pharmaceuticals |
Durham, NC |
Small Molecules, Cyclic Peptides |
| Find Therapeutics |
Saint-Laurent, QC |
GPCR-Targeting Therapeutics |
| Flamingo Therapeutics |
Leuven, Belgium |
RNA Therapeutics |
| Fractyl Health |
Burlington, MA |
Thermal ablation therapy, Gene Therapy |
| Frontera Therapeutics |
Suzhou, China |
Gene Therapy Development |
| Frontera Therapeutics |
Bedford, MA |
Gene Therapy Development |
| Genascence |
Palo Alto, CA |
Musculoskeletal Gene Therapies |
| GenEdit |
Brisbane, CA |
Nonviral CRISPR-delivery system |
| Geneos Therapeutics |
Philadelphia, PA |
Plasmid-based Neoantigen-targeted Cancer Therapies |
| Generation Bio |
Cambridge, MA |
Gene Therapy |
| Genetix Biotherapeutics |
Somerville, MA |
Gene Therapy, Cellular Extraction & Reintroduction |
| Genexine |
Seoul, Korea |
Biologics, DNA Plasmid Vaccine |
| GenKOre |
Daejeon, Korea |
Gene-editing therapies |
| GenKOre |
Seoul, Korea |
Gene-editing therapies |
| Genocury Biotech |
Shenzhen, China |
Off-the-shelf Cell & Gene Therapy |
| Genprex |
Austin, TX |
Immunogene Therapy |
| GenSight Biologics |
Paris, France |
Ophthalmic Gene Therapy |
| GenVivo |
San Marino, CA |
Proprietary Gene Delivery Technology |
| Gradalis |
Carrollton, TX |
Cancer immunotherapy, RNAi |
| Gritgen Therapeutics |
Suzhou, China |
Gene Therapy |
| HAYA Therapeutics |
San Diego, CA |
RNA-based, RNA-targeting Fibrotic Therapies |
| HAYA Therapeutics |
Lausanne, Switzerland |
RNA-based, RNA-targeting Fibrotic Therapies |
| Helix Nanotechnologies |
Boston, MA |
DNA Therapy |
| Helixmith |
Seoul, Korea |
plasmid DNA based gene therapy |
| Henovcom Bioscience |
Guangzhou, China |
Small Molecules, mRNA, 505 (b)(2) |
| HitGen |
Chengdu, China |
DNA encoded library for drug discovery |
| Holostem Tarapie Avanzate |
Modena, Italy |
Cell & Gene Therapy |
| HuidaGene Therapeutics |
Shanghai, China |
Gene Therapy, Gene editing platform, delivery vector platform |
| Hunterian Medicine |
Cambridge, MA |
CRISPR-based drug discovery |
| Hybridize Therapeutics |
Oegstgeest, Netherlands |
RNA treatments for kidney disease |
| Ibex Biosciences |
Cumberland, MD |
Biologics, Cell Therapy, Gene Therapy |
| iCell Gene Therapeutics |
Stony Brook, NY |
Gene Therapy for Cancer |
| Immorna Biotherapeutics |
Shanghai, China |
Self-Replicating RNA |
| Immuno Cure Biotech |
Hong Kong, China |
Therapeutic Antibodies, DNA Vaccines |
| Innovac Therapeutics |
Cambridge, MA |
RNA Therapeutics |
| InnoVec Biotherapeutics |
Beijing, China |
AAV-Based Gene Therapy |
| Inovio Pharmaceuticals |
San Diego, CA |
DNA Vaccines |
| Inovio Pharmaceuticals |
Plymouth Meeting, PA |
DNA Vaccines |
| Inozyme Pharma |
Boston, MA |
Enzyme Replacement Therapy |
| Interius BioTherapeutics |
Philadelphia, PA |
Novel methods for in vivo cell-specific gene delivery |
| Invectys |
Paris, France |
DNA Vaccine |
| invIOs |
Vienna, Austria |
Novel cancer immunotherapies, cell, siRNA, peptides |
| IO Biotech |
Copenhagen, Denmark |
Immuno-Oncology |
| Ionis Pharmaceuticals |
Carlsbad, CA |
RNA |
| Jaguar Gene Therapy |
Lake Forest, IL |
AAV-Based Gene Therapies |
| Junevity |
San Francisco, CA |
Long-lasting siRNA Therapies |
| Juniper Biologics |
Singapore , Singapore |
Small Molecules, Cell Therapy, Gene Therapy |
| Kailera Therapeutics |
San Diego, CA |
Peptides, Small Molecules |
| Kailera Therapeutics |
Waltham, MA |
Peptides, Small Molecules |
| Kanglin Biotechnology |
Hangzhou, China |
AAV Gene Therapy, Stem Cell Platform |
| Kelonia Therapeutics |
Boston, MA |
in vivo CAR T Gene Therapy |
| Kither Biotech |
Torino, Italy |
Therapies for the treatment of rare pulmonary diseases |
| Kolon Life Science |
Seoul, Korea |
Cell & Gene Therapy, APIs |
| Korro Bio |
Cambridge, MA |
RNA-editing Drugs |
| Kriya Therapeutics |
Redwood City, CA |
Gene Therapy |
| Kriya Therapeutics |
Morrisville, NC |
Gene Therapy |
| Krystal Biotech |
Pittsburgh, PA |
Gene Therapy |
| Lexeo Therapeutics |
New York, NY |
Gene Therapy |
| Longevity Biotech |
Philadelphia, PA |
Synthetic Peptides |
| Luxna Biotech |
Osaka, Japan |
Oligonucleotide Therapeutics |
| Lytica Therapeutics |
Cambridge, MA |
Antimicrobial peptide Design |
| Mach5 Therapeutics |
Atlanta, GA |
Gene therapies and advanced biologics |
| MAIA Biotechnology |
Chicago, IL |
Peptide Cancer Therapies |
| Mammoth Biosciences |
Brisbane, CA |
CRISPR, Gene-Editing Therapies |
| Maze Therapeutics |
South SF, CA |
Small Molecules, Gene Therapy, Antisense Oligonucleotides, Biologics |
| MBX Biosciences |
Carmel, IN |
Hormone Analogues for Rare Endocrine Diseases |
| MDimune |
Seoul, Korea |
Drug Delivery Based on Cell-Derived Vesicles |
| Medikine |
San Diego, CA |
Small Molecules, Peptide |
| MeiraGTx |
London, UK |
Gene Therapy |
| MiNA Therapeutics |
London, UK |
Small activating RNA |
| miRecule |
Gaithersburg, MD |
microRNA Therapeutics for Cancer |
| Modalis Therapeutics |
Tokyo, Japan |
Genome Editing Tools for Therapeutic Discovery |
| Modalis Therapeutics |
Waltham, MA |
Genome Editing Tools for Therapeutic Discovery |
| Moderna Therapeutics |
Melbourne, Australia |
RNA Therapies |
| Moderna Therapeutics |
Cambridge, MA |
RNA Therapies |
| Moderna Therapeutics |
Cambridge, MA |
RNA Therapies |
| Moderna Therapeutics |
Norwood, MA |
RNA Therapies |
| Moderna Therapeutics |
Harwell, UK |
RNA Therapies |
| Mustang Bio |
Worcester, MA |
Immunotherapies |
| MyoPax |
Berlin, Germany |
Cell & Gene Therapies |
| NanoCell Therapeutics |
Wayne, PA |
Gene Therapy |
| NervGen Pharma |
Vancouver, BC |
Peptide inhibitor of protein tyrosine phosphatase sigma |
| NeuExcell Therapeutics |
Philadelphia, PA |
Gene Therapy for Neural Regeneration & Repair |
| Neurogene |
New York, NY |
Genetic Therapies |
| Neurogene |
Houston, TX |
Genetic Therapies |
| Neurophth Therapeutics |
Wuhan, China |
Ophthalmology Gene Therapy |
| Nitto BioPharma |
San Diego, CA |
Drug Delivery of siRNA |
| Novartis |
Cambridge, MA |
Small Molecules, Vaccines, Biologics / Diagnostics |
| Novartis |
Mexico City, Mexico |
Small Molecules, Vaccines, Biologics |
| Novartis |
East Hanover, NJ |
Small Molecules, Vaccines, Biologics |
| Novartis |
Basel, Switzerland |
Small Molecules, Vaccines, Biologics |
| Nuevocor |
Singapore, Singapore |
AAV-based gene therapy |
| Nuntius Therapeutics |
London, UK |
mRNA Therapies |
| Nykode Therapeutics |
Oslo, Norway |
Therapeutic DNA Vaccine |
| Obsidian Therapeutics |
Cambridge, MA |
Cell & Gene Therapies |
| Ochre Bio |
Oxford, UK |
siRNA liver drugs |
| Oculgen |
Nanshan District, China |
Gene and cell therapies, biologics, vaccines |
| OliPass |
Gyeonggi, Korea |
Peptide nucleic acid derivatives |
| OliX Pharmaceuticals |
Seongnam, Korea |
RNAi Treatments |
| Oncogenuity |
Bay Harbor Islands, FL |
Oligonucleotide platform for the treatment of genetically driven cancers |
| Oncotherapy Science |
Kawasaki, Japan |
Small Molecule, peptides, antibody therapies, contract analytical |
| Onodera |
Kanagawa, Japan |
Gene Therapy |
| Opus Genetics |
Raleigh, NC |
Ophthalmology Gene Therapy |
| Orbital Therapeutics |
Cambridge, MA |
RNA technology (not RNAi) |
| Orchard Therapeutics |
Boston, MA |
Ex-vivo autologous hematopoietic stem cell gene therapy |
| Orchard Therapeutics |
London, UK |
Ex-vivo autologous hematopoietic stem cell gene therapy |
| Orna Therapeutics |
Watertown, MA |
oRNA, Delivery |
| Pantherna Therapeutics |
Hennigsdorf, Germany |
Nanoparticle Delivery for mRNA drugs |
| Passage Bio |
Philadelphia, PA |
Gene Therapy |
| PEEL Therapeutics |
Salt Lake City, UT |
Nature-inspired Cancer Therapies |
| Peptilogics |
Pittsburgh, PA |
Peptide Therapeutics |
| Pfizer |
La Jolla, CA |
Peptides, Monoclonal Antibodies |
| Pfizer |
Durham, NC |
Small Molecules, Vaccines, Biologics |
| Pfizer |
Bothell, WA |
Small Molecules, Vaccines, Biologics |
| Pinion Immunotherapeutics |
North Bethesda, MD |
mRNA Vaccine Technology |
| Poolbeg Pharma |
London, UK |
Developing drugs to sell off |
| Poseida Therapeutics |
San Diego, CA |
Genome Editing Technologies |
| Precigen |
Germantown, MD |
Cell & Gene Therapy |
| Priavoid |
Düsseldorf, Germany |
All-d-peptides |
| ProQR Therapeutics |
Cambridge, MA |
Oligonucleotide Therapy |
| ProQR Therapeutics |
Leiden, Netherlands |
Oligonucleotide Therapy |
| Protagonist Therapeutics |
Brisbane, Australia |
Oral peptides |
| Protagonist Therapeutics |
Newark, CA |
Oral peptides for GI indications |
| Protelight Pharmaceuticals |
Jiangyin, China |
Peptide and Small Molecules Therapies |
| PTC Therapeutics |
Warren, NJ |
Small Molecules, Gene Therapy |
| Purespring Therapeutics |
London, UK |
Gene Therapy for Kidney Disease |
| PYC Therapeutics |
Nedlands, Australia |
Peptide drug discovery |
| Ractigen Therapeutics |
Nantong, China |
Small activating RNA |
| Radar Therapeutics |
, |
Smart Programmable Medicines Using Molecular RNA Sensors |
| Ray Therapeutics |
Berkeley, CA |
Optogenetic Gene Therapy |
| Recbio Technology |
Taizhou, China |
mRNA Covid Vaccine |
| ReCode Therapeutics |
Menlo Park, CA |
Nucleic Acid Therapeutic Delivery |
| Regel Therapeutics |
Berkeley, CA |
AAV gene delivery |
| Regel Therapeutics |
Cambridge, MA |
AAV gene delivery |
| ReGenX Biosciences |
Rockville, MD |
Gene Therapy, Biologics |
| Rejuve Therapeutics |
Beltsville, MD |
Gene therapy drug development company researching senescent cell solutions. |
| Rejuvenate Bio |
San Diego, CA |
Gene Therapy for Aging |
| Remedium Bio |
Needham, MA |
Gene Therapy |
| Repertoire Immune Medicines |
Cambridge, MA |
Cell & Peptide-Based Therapies |
| Replicate Bioscience |
San Diego, CA |
Preventing oncology drug resistance |
| Rhythm Pharmaceuticals |
Boston, MA |
Peptide Therapeutics |
| Ribocure Pharmaceuticals |
Mölndal, Sweden |
RNA Therapeutics |
| Ribomic |
Tokyo , Japan |
Aptamers |
| RiboX Therapeutics |
Shanghai, China |
Circular RNA |
| RinuaGene Biotechnology |
Suzhou, China |
mRNA Therapies |
| Risen Pharma Tech |
Shanghai, China |
Small Molecules, siRNA, Combination Therapies |
| Risen Pharma Tech |
Suzhou, China |
Small Molecules, siRNA, Combination Therapies |
| Rithim Biologics |
Woodbine, MD |
Gene Therapy for Tachycardias |
| Rocket Pharmaceuticals |
Cranbury, NJ |
Gene Therapies |
| Rona Therapeutics |
Shanghai, China |
RNA Therapeutics Platform |
| Sana Biotechnology |
Seattle, WA |
Cell & Gene Therapies |
| SanegeneBio |
Woburn, MA |
siRNA Drug Discovery |
| Sapience Therapeutics |
Tarrytown, NY |
Peptide-based Therapies for cancers |
| Sciwind Biosciences |
Hangzhou, China |
Oral peptide delivery |
| Senti Biosciences |
South SF, CA |
Gene Circuits; Cell & Gene Therapies |
| Seragon Biosciences |
Irvine, CA |
Small Molecules, Gene Therapy |
| Shape Therapeutics |
Seattle, WA |
RNA-editing gene therapy |
| Shenogen Pharma |
Beijing, China |
Small Molecules, Biologics, Viral |
| Silence Therapeutics |
Berlin, Germany |
RNAi |
| Silence Therapeutics |
Hoboken, NJ |
RNAi |
| Silence Therapeutics |
London, UK |
RNAi |
| SineuGene |
Beijing, China |
Gene Therapy |
| Siren Biotechnology |
San Francisco, CA |
AAV Immuno-Gene Therapy |
| Sirnaomics |
Suzhou, China |
RNAi Therapeutics |
| Sirnaomics |
Germantown, MD |
RNAi Therapeutics |
| SNIPR BIOME |
Copenhagen, Denmark |
CRISPR for microbiome management, genetically-modified bacteriophages |
| Solid Biosciences |
Charlestown, MA |
Gene Therapy, Devices, Biologics, Small Molecules all for DMD |
| SparingVision |
Paris, France |
Retinal Gene Therapy Treatments |
| SparingVision |
Philadelphia, PA |
Retinal Gene Therapy Treatments |
| Spirovant Sciences |
Philadelphia, PA |
Gene Therapy - Lung Diseases |
| SpliSense |
Jerusalem, Israel |
Antisense Oligonucleotides |
| Starna Therapeutics |
Suzhou, China |
mRNA vaccine, therapies |
| Sterna Biologicals & KG |
Marburg, Germany |
Antisense Molecule - DNAzyme |
| Stoke Therapeutics |
Bedford, MA |
Antisense Oligonucleotide Medicines |
| Strand Therapeutics |
Boston, MA |
Gene Therapy |
| STRM.BIO |
Cambridge, MA |
Extracellular vesicles (EVs) to deliver gene therapies |
| Suzhou Ribo Life Science Company |
Kunshan, China |
RNAi |
| Switch Therapeutics |
South SF, CA |
RNAi Therapies |
| Sylentis |
Madrid, Spain |
RNAi Treatments |
| TAGCyx Biotechnologies |
Tokyo, Japan |
Oligonucleotide Drug Discovery Platform |
| Taysha Gene Therapies |
Dallas, TX |
Adeno-associated virus gene therapies |
| Tenaya Therapeutics |
South SF, CA |
Cardiovascular Therapeutics |
| Tevard Biosciences |
Cambridge, MA |
tRNA-based Gene Therapies |
| Therorna |
Beijing, China |
RNA Therapies |
| TransCode Therapeutics |
Newton, MA |
RNA Delivery, Small Molecule |
| Transgene |
Illkirch-Graffenstaden, France |
Viral Vector Therapeutics, Gene Therapy |
| Transgene |
Boston, MA |
Viral Vector Therapeutics, Gene Therapy |
| Treeway |
Tilburg, Netherlands |
Small Molecules, Gene Therapy |
| Tune Therapeutics |
Durham, NC |
Epigenetic modification to modulate gene expression |
| Tune Therapeutics |
Seattle, WA |
Epigenetic modification to modulate gene expression |
| Turn Biotechnologies |
Mountain View, CA |
mRNA Therapies |
| Ultragenyx Pharmaceutical |
Brisbane, CA |
Small Molecules, Biologics |
| Ultragenyx Pharmaceutical |
Novato, CA |
Small Molecules, Biologics, Gene Therapy, mRNA, Antisense Oligo |
| Ultragenyx Pharmaceutical |
Bedford, MA |
Small Molecules, Biologics, Gene Therapy, mRNA, Antisense Oligo |
| Ultragenyx Pharmaceutical |
Somerville, MA |
Small Molecules, Biologics |
| Ultragenyx Pharmaceutical |
Woburn, MA |
Small Molecules, Biologics |
| uniQure |
Amsterdam, Netherlands |
Gene Therapy |
| Unnatural Products |
Santa Cruz, CA |
Macrocylic Peptides plus AI |
| Valerio Therapeutics |
Paris, France |
Orphan Diseases, Decoy Oligonucleotides |
| Valo Therapeutics |
Helsinki, Finland |
Oncolytic Virus, Peptide |
| VectorY Therapeutics |
Amsterdam, Netherlands |
Vectorized Antibodies |
| VeonGen Therapeutics |
Planegg, Germany |
AAV Gene Therapy |
| Verrica Pharmaceuticals |
West Chester, PA |
Topical therapies |
| Versameb |
Basel, Switzerland |
RNA Therapeutics |
| Vico Therapeutics |
Leiden, Netherlands |
Oligonucleotide based RNA modulating therapeutics |
| Vigeo Therapeutics |
Cambridge, MA |
Biologics for Cancer |
| Vir Biotechnology |
San Francisco, CA |
Infectious disease therapies |
| Vir Biotechnology |
Bellinzona, Switzerland |
Infectious disease therapies |
| Visirna Therapeutics |
Shanghai, China |
RNAi Therapeutics: siRNA Drugs |
| Vivet Therapeutics |
Paris, France |
Gene Therapy for Orphan Diseases |
| Voyager Therapeutics |
Lexington, MA |
AAV capsid Gene Therapy |
| WaVe Life Sciences |
Kagoshima, Japan |
Stereopure oligonucleotides |
| WaVe Life Sciences |
Cambridge, MA |
Stereopure oligonucleotides |
| Westlake Genetech |
Hangzhou, China |
AI-powered Gene Therapy Development |
| Xequel Bio |
Mount Pleasant, SC |
Peptide for Injury Healing |
| Xequel Bio |
Fort Worth, TX |
Peptide for Injury Healing |
| XyloCor Therapeutics |
King of Prussia, PA |
Gene Therapy |
| Zata Pharmaceuticals |
Worcester, MA |
RNA, DNA Therapeutics |
| Zealand Pharma |
Soborg, Denmark |
Peptide Drugs |
| Zhongmou Therapeutics |
Wuhan, China |
AAV-Based Optogenetic Gene Therapies for Ocular Diseases |
| Ziphius Vaccines |
Merelbeke, Belgium |
Self-amplifying RNA Vaccine |