Protagonist Therapeutics |
St Lucia, Brisbane, Australia |
Oral peptides |
Ever Neuro Pharma |
Unterach, Austria |
Small molecule/peptide for neurology, small molecule injectables for cancer, anesthetic, women's health |
Arbutus Biopharma |
Vancouver, BC |
RNAi |
Sierra Oncology |
Vancouver, BC |
DNAi |
Apitope |
Diepenbeek, Belgium |
Antigen specific therapeutic peptides |
Scribe Therapeutics |
Alameda, CA |
CRISPR platform |
GenEdit |
Berkeley, CA |
Nonviral CRISPR-delivery system |
Ionis Pharmaceuticals |
Carlsbad, CA |
RNA |
4D Molecular Therapeutics |
Emeryville, CA |
Gene Therapy |
Dynavax Technologies |
Emeryville, CA |
DNA Therapeutics |
Orchard Therapeutics |
Foster City, CA |
Ex-vivo autologous hematopoietic stem cell gene therapy |
Spotlight Therapeutics |
Hayward, CA |
In vivo Gene Editing |
Avidity Biosciences |
La Jolla, CA |
Antibody-Oligonucleotide Conjugates |
CytRx |
Los Angeles, CA |
Small Molecules, DNA |
Circuit Therapeutics |
Menlo Park, CA |
Optogenetics |
CohBar |
Menlo Park, CA |
Mitochondrial-Derived Peptides |
Orchard Therapeutics |
Menlo Park, CA |
Ex-vivo autologous hematopoietic stem cell gene therapy |
Turn Biotechnologies |
Mountain View, CA |
mRNA Therapies |
Protagonist Therapeutics |
Newark, CA |
Oral peptides for GI indications |
Quark Pharmaceuticals |
Newark, CA |
SiRNA, Drug Discovery |
Alzamend Neuro |
Newport Beach, CA |
Alzheimer's Treatment |
Ultragenyx Pharmaceutical |
Novato, CA |
Small Molecules, Biologics |
Bioneer |
Oakland, CA |
Protein Synthesis Equipment & Reagents. Plans for drug discovery. |
Arrowhead Pharmaceuticals |
Pasadena, CA |
RNAi |
Adverum Biotechnologies |
Redwood City, CA |
Adeno-Associated Virus Delivery, Gene Therapy |
Kriya Therapeutics |
Redwood City, CA |
Gene Therapy |
Abintus Bio |
San Diego, CA |
Gene Therapy |
Arcturus Therapeutics |
San Diego, CA |
Lipid nanoparticle (LNP) siRNA drug delivery systems |
Cidara Therapeutics |
San Diego, CA |
Small molecules, peptide |
CODEX DNA |
San Diego, CA |
Synthetic DNA |
Eli Lilly |
San Diego, CA |
Biologics Discovery |
Empirico |
San Diego, CA |
Genetics-Based Drug Discovery |
Helixmith |
San Diego, CA |
plasmid DNA based gene therapy |
Inovio Pharmaceuticals |
San Diego, CA |
DNA Vaccines |
Locanabio |
San Diego, CA |
RNA-targeting gene therapy |
Nitto BioPharma |
San Diego, CA |
Drug Delivery of siRNA |
Oxford BioMedica |
San Diego, CA |
Gene-based Medicines |
Peptide Logic |
San Diego, CA |
Peptide-Antibody Conjugates |
Pfizer |
San Diego, CA |
Peptides, Monoclonal Antibodies |
Poseida Therapeutics |
San Diego, CA |
Genome Editing Technologies |
Regulus Therapeutics |
San Diego, CA |
MicroRNAs |
Aligos Therapeutics |
San Francisco, CA |
Therapies for hepatologic diseases and viral infections |
Apellis Pharmaceuticals |
San Francisco, CA |
Cyclic peptide analog |
DNALite Therapeutics |
San Francisco, CA |
Gene Therapy |
Vir Biotechnology |
San Francisco, CA |
Infectious disease therapies |
Ambys Medicines |
South SF, CA |
Liver cell, gene, drug therapies |
Circle Pharma |
South SF, CA |
Macrocyclic Therapeutics |
Coda Biotherapeutics |
South SF, CA |
Gene Therapy |
Encoded Therapeutics |
South SF, CA |
Gene Therapy |
Maze Therapeutics |
South SF, CA |
Genetic Modifiers of Disease |
Tenaya Therapeutics |
South SF, CA |
Cardiovascular Therapeutics |
Bachem |
Torrance, CA |
Peptides, APIs |
Emmaus Life Sciences |
Torrance, CA |
Oral amino acid treatment |
EdiGene (2) |
Beijing, China |
Gene Editing Technologies |
Shenogen Pharma |
Beijing, China |
Small Molecules, Biologics, Viral |
Veraptus |
Changsha, China |
Aptamers |
HitGen |
Chengdu, China |
DNA encoded library for drug discovery |
Adlai Nortye |
Hangzhou, China |
Cancer & Metabolic Disease Treatments |
TOT Biopharm |
Jiangsu, China |
Biosimilars, Antibodies, Gene Therapy, Vaccines |
Suzhou Ribo Life Science Company |
Kunshan, China |
RNAi |
Frontier Biotechnologies |
Nanjing, China |
Long-acting peptides, APIS |
Sirnaomics |
Suzhou, China |
RNAi Therapeutics |
Viridian Therapeutics |
Boulder, CO |
MicroRNA |
SNIPR Biome |
Copenhagen, Denmark |
CRISPR for microbiome management |
Zealand Pharma |
Soborg, Denmark |
Peptide Drugs |
Herantis Pharma |
Espoo, Finland |
Biologic for Parkinson's, gene therapy for secondary lymphedema |
Valo Therapeutics |
Helsinki, Finland |
Oncolytic Virus, Peptide |
AGTC |
Alachua, FL |
Gene Therapy |
Lacerta Therapeutics |
Alachua, FL |
AAV Gene Therapy |
Transgene |
Illkirch-Graffenstaden, France |
Viral Vector Therapeutics, Gene Therapy |
PDC*line Pharma |
La Tronche, France |
Novel class of off-the-shelf cancer immunotherapies based on a proprietary Plasmacytoid Dendritic Cell line pre-loaded with peptides |
Transgene |
Lyon, France |
Viral Vector Therapeutics, Gene Therapy |
Eli Lilly |
Neuilly-sur-Seine, France |
Small Molecules, Biologics |
Inotrem |
PARIS, France |
Peptide Therapy |
Invectys |
Paris, France |
DNA Vaccine |
Vivet Therapeutics |
Paris, France |
Gene Therapy for Orphan Diseases |
Smartox Biotechnology |
Saint Martin d’Hères, France |
Peptide-based drug discovery |
InnoSkel |
Valbonne, France |
Therapies for Rare Skeletal Diseases |
Inotrem |
Vandoeuvre-lès-Nancy, France |
Peptide Therapy |
Berlin Cures |
Berlin, Germany |
Aptamer for Cardio Indication |
Silence Therapeutics |
Berlin, Germany |
RNAi |
CureVac |
Frankfurt, Germany |
MRNA treatments |
Evotec |
Hamburg, Germany |
Contract drug discovery & development offering integrated solutions from Target ID through to Clinic |
Cardior Pharmaceuticals |
Hanover, Germany |
Ncrna inhibitor for myocardial infarction |
Pantherna Therapeutics |
Hennigsdorf, Germany |
Nanoparticle Delivery for mRNA drugs |
BioNTech |
Idar-Oberstein, Germany |
Biologics |
BioNTech |
Mainz, Germany |
Biologics |
Ethris |
Planegg, Germany |
MRNA-based therapies |
BioNTech |
Planegg-Martinsried, Germany |
Biologics |
Freeline Therapeutics |
Planegg-Steinkirchen, Germany |
Protein replacement via Gene Therapy |
CureVac |
Tübingen, Germany |
MRNA treatments |
Exicure |
Chicago, IL |
Spherical Nucleic Acid |
MAIA Biotechnology |
Chicago, IL |
Peptide Cancer Therapies |
Eli Lilly |
Indianapolis, IN |
Small Molecules, Biologics |
Eli Lilly |
Kinsale, Ireland |
Small Molecules, Biologics |
BioLineRx |
Modi’in, Israel |
Small Molecules, Biologics |
Quark Pharmaceuticals |
Ness Ziona, Israel |
SiRNA, Drug Discovery |
Holostem Tarapie Avanzate |
Modena, Italy |
Cell & Gene Therapy |
Eli Lilly |
Sesto Fiorentino, Italy |
Small Molecules, Biologics |
WaVe Life Sciences |
Kagoshima, Japan |
Nucleic acid therapies |
Luxna Biotech |
Osaka, Japan |
Oligonucleotide Therapeutics |
Epsilon Molecular Engineering |
Saitama, Japan |
Heavy chain single domain antibodies |
Ribomic |
Tokyo , Japan |
Aptamers |
Sosei Group |
Tokyo, Japan |
Umbrella Company |
OliPass |
Gyeonggi, Korea |
Peptide nucleic acid derivatives |
OliX Pharmaceuticals |
Gyeonggi, Korea |
RNAi Treatments |
Helixmith |
Seoul, Korea |
plasmid DNA based gene therapy |
Kolon Life Science |
Seoul, Korea |
Cell & Gene Therapy, APIs |
Aptabio Therapeutics |
Yongin, Korea |
Aptamer-drug Conjugates |
Apellis Pharmaceuticals |
Crestwood, KY |
Cyclic peptide analog |
Homology Medicines |
Bedford, MA |
Gene-editing via homologous recombination |
Stoke Therapeutics |
Bedford, MA |
Antisense Oligonucleotide Medicines |
Akcea Therapeutics |
Boston, MA |
RNA Antisense Technology |
Akouos |
Boston, MA |
Gene Therapy for Hearing Disorders |
Atalanta Therapeutics |
Boston, MA |
RNAi therapeutics |
CureVac |
Boston, MA |
MRNA treatments |
Inozyme Pharma |
Boston, MA |
Enzyme Replacement Therapy |
Orchard Therapeutics |
Boston, MA |
Ex-vivo autologous hematopoietic stem cell gene therapy |
Rhythm Pharmaceuticals |
Boston, MA |
Peptide Therapeutics |
Transgene |
Boston, MA |
Viral Vector Therapeutics, Gene Therapy |
AGTC |
Cambridge, MA |
Gene Therapy |
Alnylam Pharmaceuticals |
Cambridge, MA |
RNAi |
Apic Bio |
Cambridge, MA |
Gene Therapy |
AVROBIO |
Cambridge, MA |
Cellular & Gene Therapies |
Axcella Health |
Cambridge, MA |
Amino acid mediated therapeutics |
bluebird bio |
Cambridge, MA |
Gene Therapy, Cellular Extraction & Reintroduction |
Dicerna Pharmaceuticals |
Cambridge, MA |
RNAi |
Editas Medicine |
Cambridge, MA |
Genome Editing Therapies (CRISPR) |
Eli Lilly |
Cambridge, MA |
Small Molecules, Biologics |
FerGene |
Cambridge, MA |
Treatment for non-muscle invasive bladder cancer |
Gemini Therapeutics |
Cambridge, MA |
Genetically-targeted Ophthalmology Medicine |
Generation Bio |
Cambridge, MA |
Gene Therapy |
Intellia Therapeutics |
Cambridge, MA |
Therapeutic gene editing (CRISPR) |
Korro Bio |
Cambridge, MA |
RNA-editing Drugs |
Moderna Therapeutics |
Cambridge, MA |
RNA Therapies |
Moderna Therapeutics |
Cambridge, MA |
RNA Therapies |
Moderna Therapeutics |
Cambridge, MA |
RNA Therapies |
Moma Therapeutics |
Cambridge, MA |
Enzymes - Molecular Machines |
Obsidian Therapeutics |
Cambridge, MA |
Cell & Gene Therapies |
ProQR Therapeutics |
Cambridge, MA |
Oligonucleotide Therapy |
SmartPharm Therapeutics |
Cambridge, MA |
Production of biologics within patients via gene therapy |
Solid Biosciences |
Cambridge, MA |
Gene Therapy, Devices, Biologics, Small Molecules all for DMD |
Strand Therapeutics |
Cambridge, MA |
Gene Therapy |
Sumitomo Dainippon Pharma Oncology |
Cambridge, MA |
RNAi, Small Molecules |
Tevard Biosciences |
Cambridge, MA |
tRNA-based Gene Therapies |
Verve Therapeutics |
Cambridge, MA |
Gene-editing Treatments |
Vigeo Therapeutics |
Cambridge, MA |
Biologics for Cancer |
Voyager Therapeutics |
Cambridge, MA |
CNS Gene Therapy |
Bicycle Therapeutics |
Lexington, MA |
Peptides |
LogicBio Therapeutics |
Lexington, MA |
Gene Therapy |
Translate Bio |
Lexington, MA |
Non-Coding RNA Targeting |
uniQure |
Lexington, MA |
Gene Therapy |
WaVe Life Sciences |
Lexington, MA |
Nucleic acid therapies |
Phio Pharmaceuticals |
Marlborough, MA |
RNAi |
SOLA Biosciences |
Natick, MA |
Gene Therapies for Protein Misfolding Diseases |
entrinsic bioscience |
Norwood, MA |
Amino Acid Treatments |
Moderna Therapeutics |
Norwood, MA |
RNA Therapies |
Apellis Pharmaceuticals |
Waltham, MA |
Cyclic peptide analog |
Viridian Therapeutics |
Waltham, MA |
MicroRNA |
Aileron Therapeutics |
Watertown, MA |
Perpetually Active Peptides |
Zata Pharmaceuticals |
Worcester, MA |
RNA, DNA Therapeutics |
Sirnaomics |
Gaithersburg, MD |
RNAi Therapeutics |
American Gene Technologies |
Rockville, MD |
Gene Therapy and Immunotherapy Company. Lentiviral Vector Platform and Indication-Specific Technologies. Lead Therapeutics for an HIV Cure, Liver Cancer Cure, and PKU therapy |
ReGenX Biosciences |
Rockville, MD |
Gene Therapy, Biologics |
Eli Lilly |
San José, Mexico |
Small Molecules, Biologics |
ONL Therapeutics |
Ann Arbor, MI |
Small molecule peptide |
Atsena Therapeutics |
Durham, NC |
Gene Therapy |
bluebird bio |
Durham, NC |
Gene Therapy, Cellular Extraction & Reintroduction |
Fennec Pharma |
Durham, NC |
Small Molecules, Cyclic Peptides |
Precision BioSciences |
Durham, NC |
Genome-editing enzymes, CAR-T |
Sio Gene Therapies |
Durham, NC |
Gene Therapy for Neurodegenerative Indications |
Kriya Therapeutics |
Morrisville, NC |
Gene Therapy |
Arthrogen |
Amsterdam, Netherlands |
Gene therapy for rheumatoid arthritis |
uniQure |
Amsterdam, Netherlands |
Gene Therapy |
Amarna Therapeutics |
Leiden, Netherlands |
Viral Gene Delivery Platform |
Amylon Therapeutics |
Leiden, Netherlands |
RNA-based therapies |
ProQR Therapeutics |
Leiden, Netherlands |
Oligonucleotide Therapy |
Chondropeptix |
Maastricht, Netherlands |
Peptide for cartilage improvement |
InteRNA Technologies |
Nijmegen, Netherlands |
MiRNA Therapeutics |
Treeway |
Tilburg, Netherlands |
Small Molecules, Gene Therapy |
InteRNA Technologies |
Utrecht, Netherlands |
MiRNA Therapeutics |
IVERIC Bio |
Cranbury, NJ |
Aptamers, Biologics |
Fixx Pharmaceuticals |
Las Vegas, NV |
Developing a cure for Hemophilia through the use of CRISPR gene editing |
Sapience Therapeutics |
Harrison, NY |
Peptide-based Therapies for cancers |
Lodo Therapeutics |
New York, NY |
Cyclic Peptide |
Neurogene |
New York, NY |
Genetic Therapies |
Prevail Therapeutics |
New York, NY |
AAV-based gene therapies |
Protagenic Therapeutics |
New York, NY |
Neuro-Active Peptides |
Rocket Pharmaceuticals |
New York, NY |
Gene Therapies |
Sio Gene Therapies |
New York, NY |
Gene Therapy for Neurodegenerative Indications |
|
ZZ, NY |
Cell-permeable Peptide |
Abeona Therapeutics |
Cleveland, OH |
Therapies for Sanfilippo (SF) Syndrome Type A and Type B. |
ExonanoRNA |
Columbus, OH |
RNA nanoparticles, therapies |
AVROBIO |
Toronto, ON |
Cellular & Gene Therapies |
Deep Genomics |
Toronto, ON |
AI-discovery, Oligonucleotide Therapies |
SwanBio Therapeutics |
Bala Cynwyd, PA |
Gene Therapy |
Formula Pharmaceuticals |
Berwyn, PA |
Oncology Drug Development |
Gyroscope Therapeutics |
King of Prussia, PA |
Gene Therapy |
Limelight Bio |
Philadelphia, PA |
Gene Therapy |
Passage Bio |
Philadelphia, PA |
Gene Therapy |
Spark Therapeutics |
Philadelphia, PA |
Singe Dose Gene Therapy |
XyloCor Therapeutics |
Philadelphia, PA |
Gene Therapy |
Krystal Biotech |
Pittsburgh, PA |
Gene Therapy |
Geneos Therapeutics |
Plymouth Meeting, PA |
Plasmid-based Neoantigen-targeted Cancer Therapies |
Inovio Pharmaceuticals |
Plymouth Meeting, PA |
DNA Vaccines |
Windtree Therapeutics |
Warrington, PA |
Peptides |
Eli Lilly |
Carolina, PR |
Recombinant Insulin |
Eli Lilly |
Mayaguez, PR |
Small Molecules, Biologics |
Carmine Therapeutics |
Singapore, Singapore |
Medicines based on red blood cell extracellular vesicles (RBCEVs), for the delivery of novel therapeutic modalities that include nucleic acids |
Eli Lilly |
Alcobendas, Spain |
Small Molecules, Biologics |
Sylentis |
Madrid, Spain |
RNAi Treatments |
Bachem |
Bubendorf, Switzerland |
Peptides, APIs |
AMAL Therapeutics |
Geneva, Switzerland |
Therapeutic Vaccines |
Antion Biosciences |
Geneva, Switzerland |
Gene & Cell Therapy |
Gene Signal |
Lausanne, Switzerland |
Biologics |
IBSA Institut Biochimique |
Lugano, Switzerland |
Various Treatments and Nutraceuticals |
DiNAQOR |
Pfäffikon , Switzerland |
Gene Therapy for Heart Conditions |
Redbiotec |
Schlieren, Switzerland |
Various Biologic Modalities |
Alnylam Pharmaceuticals |
Zug, Switzerland |
RNAi |
Bio-Path Holdings |
Bellaire, TX |
Antisense DNA therapeutics |
Neurogene |
Houston, TX |
Genetic Therapies |
Base Pair Biotechnologies |
Pearland, TX |
Aptamers and related Services |
Immunocore |
Abingdon, UK |
T Cell Receptor Fragment |
Eli Lilly |
Basingstoke, UK |
Small Molecules, Biologics |
Bicycle Therapeutics |
Cambridge, UK |
Peptides |
Apitope |
Chepstow, UK |
Antigen specific therapeutic peptides |
DiNAQOR |
London, UK |
Gene Therapy for Heart Conditions |
Enara Bio |
London, UK |
Dark Antigens to deliver targeted off-the-shelf cancer vaccines and other immunotherapies for treating and preventing cancer |
Orchard Therapeutics |
London, UK |
Ex-vivo autologous hematopoietic stem cell gene therapy |
Silence Therapeutics |
London, UK |
RNAi |
Alnylam Pharmaceuticals |
Maidenhead, UK |
RNAi |
Oxford Biomedica |
Oxford, UK |
Gene-based Medicines |
Valo Therapeutics |
Oxford, UK |
Oncolytic Virus, Peptide |
Freeline Therapeutics |
Stevenage, UK |
Protein replacement via Gene Therapy |
Gyroscope Therapeutics |
Stevenage, UK |
Gene Therapy |
Sumitomo Dainippon Pharma Oncology |
Lehi, UT |
RNAi, Small Molecules |
bluebird bio |
Seattle, WA |
Gene Therapy, Cellular Extraction & Reintroduction |
Lodo Therapeutics |
Seattle, WA |
Cyclic Peptide |
Shape Therapeutics |
Seattle, WA |
RNA-editing gene therapy |
Arrowhead Pharmaceuticals |
Madison, WI |
RNAi |