Protagonist Therapeutics |
Brisbane, Australia |
Oral peptides |
PYC Therapeutics |
Nedlands, Australia |
Peptide drug discovery |
invIOs |
Vienna, Austria |
Novel cancer immunotherapies, cell, siRNA, peptides |
Symvivo |
Burnaby, BC |
Bacterial-based gene delivery platform |
Nanovation Therapeutics |
Vancouver, BC |
Gene Therapy |
NervGen Pharma |
Vancouver, BC |
Peptide inhibitor of protein tyrosine phosphatase sigma |
Flamingo Therapeutics |
, Belgium |
RNA Therapeutics |
Aelin Therapeutics |
Leuven, Belgium |
Peptide-based Biologics |
Ziphius Vaccines |
Merelbeke, Belgium |
Self-amplifying RNA Vaccine |
Aelin Therapeutics |
Zwijnaarde, Belgium |
Peptide-based Biologics |
Regel Therapeutics |
Berkeley, CA |
AAV gene delivery |
Mammoth Biosciences |
Brisbane, CA |
CRISPR, Gene-Editing Therapies |
Ultragenyx Pharmaceutical |
Brisbane, CA |
Small Molecules, Biologics |
Ionis Pharmaceuticals |
Carlsbad, CA |
RNA |
PYC Therapeutics |
Carlsbad, CA |
Peptide drug discovery |
4D Molecular Therapeutics |
Emeryville, CA |
Gene Therapy |
Dynavax Technologies |
Emeryville, CA |
Synthetic oligonucleotides vaccines |
Spotlight Therapeutics |
Hayward, CA |
In vivo Gene Editing |
Urovant Sciences |
Irvine, CA |
Small Molecule, Gene Therapy |
Avidity Biosciences |
La Jolla, CA |
Antibody-Oligonucleotide Conjugates |
Pfizer |
La Jolla, CA |
Peptides, Monoclonal Antibodies |
DiNAQOR |
Laguna Hills, CA |
Gene Therapy for Heart Conditions |
Avellino Laboratories |
Menlo Park, CA |
Gene Therapy, Molecular Diagnostics |
CohBar |
Menlo Park, CA |
Mitochondrial-Derived Peptides |
Medikine |
Menlo Park, CA |
Small Molecules, Peptide |
Turn Biotechnologies |
Mountain View, CA |
mRNA Therapies |
Protagonist Therapeutics |
Newark, CA |
Oral peptides for GI indications |
Alzamend Neuro |
Newport Beach, CA |
Alzheimer's Treatment |
Ultragenyx Pharmaceutical |
Novato, CA |
Small Molecules, Biologics, Gene Therapy, mRNA, Antisense Oligo |
Genascence |
Palo Alto, CA |
Musculoskeletal Gene Therapies |
Arrowhead Pharmaceuticals |
Pasadena, CA |
RNAi |
Adverum Biotechnologies |
Redwood City, CA |
Adeno-Associated Virus Delivery, Gene Therapy |
Kriya Therapeutics |
Redwood City, CA |
Gene Therapy |
Abintus Bio |
San Diego, CA |
Gene Therapy |
ADARx Pharmaceuticals |
San Diego, CA |
RNA Therapeutics |
Arcturus Therapeutics |
San Diego, CA |
Lipid nanoparticle (LNP) mRNA drug delivery systems |
BioNTech |
San Diego, CA |
mRNA, Vaccines, Biologics |
Cidara Therapeutics |
San Diego, CA |
Small molecules, peptide |
Creyon Bio |
San Diego, CA |
Oligonucleotide-based Medicines |
Eli Lilly |
San Diego, CA |
Biologics Discovery |
HAYA Therapeutics |
San Diego, CA |
RNA-based, RNA-targeting Fibrotic Therapies |
Inovio Pharmaceuticals |
San Diego, CA |
DNA Vaccines |
Kate Therapeutics |
San Diego, CA |
AAV-based gene therapy for muscle disease |
Locanabio |
San Diego, CA |
RNA-targeting gene therapy |
Nitto BioPharma |
San Diego, CA |
Drug Delivery of siRNA |
Ocelot Bio |
San Diego, CA |
Peptide therapeutic to treat complications of end-stage liver disease |
Peptide Logic |
San Diego, CA |
Peptide-Antibody Conjugates |
Poseida Therapeutics |
San Diego, CA |
Genome Editing Technologies |
Regulus Therapeutics |
San Diego, CA |
MicroRNAs |
Replay |
San Diego, CA |
HSV Vector Gene Therapies |
Replicate Bioscience |
San Diego, CA |
Preventing oncology drug resistance |
Apellis Pharmaceuticals |
San Francisco, CA |
Cyclic peptide analog |
DNALite Therapeutics |
San Francisco, CA |
Gene Therapy |
Excision BioTherapeutics |
San Francisco, CA |
Gene Editing |
Ray Therapeutics |
San Francisco, CA |
Optogenetic Gene Therapy |
Vir Biotechnology |
San Francisco, CA |
Infectious disease therapies |
Unnatural Products |
Santa Cruz, CA |
Macrocylic Peptides plus AI |
Aligos Therapeutics |
South SF, CA |
Therapies for hepatologic diseases and viral infections |
Attralus |
South SF, CA |
Amyloidosis Treatments |
Circle Pharma |
South SF, CA |
Macrocyclic Therapeutics |
Encoded Therapeutics |
South SF, CA |
Gene Therapy |
GenEdit |
South SF, CA |
Nonviral CRISPR-delivery system |
Maze Therapeutics |
South SF, CA |
Small Molecules, Gene Therapy, Antisense Oligonucleotides, Biologics |
Senti Biosciences |
South SF, CA |
Gene Circuits; Cell & Gene Therapies |
SonoThera |
South SF, CA |
Ultrasound-Guided Gene Therapy |
Switch Therapeutics |
South SF, CA |
RNAi Therapies |
Tenaya Therapeutics |
South SF, CA |
Cardiovascular Therapeutics |
Capsida Biotherapeutics |
Thousand Oaks, CA |
AAV Gene Therapy |
Emmaus Life Sciences |
Torrance, CA |
Oral amino acid treatment |
Shenogen Pharma |
Beijing, China |
Small Molecules, Biologics, Viral |
Veraptus |
Changsha, China |
Aptamers |
HitGen |
Chengdu, China |
DNA encoded library for drug discovery |
Exegenesis Bio |
Hangzhou, China |
Gene Therapy |
Sciwind Biosciences |
Hangzhou, China |
Oral peptide delivery |
Immuno Cure Biotech |
Hong Kong, China |
Therapeutic Antibodies, DNA Vaccines |
Suzhou Ribo Life Science Company |
Kunshan, China |
RNAi |
Ractigen Therapeutics |
Nantong, China |
Small activating RNA |
Belief BioMed |
Shanghai, China |
AAV-delivered Gene Therapies |
HuidaGene Therapeutics |
Shanghai, China |
Gene Therapy, Gene editing platform, delivery vector platform |
Immorna Biotherapeutics |
Shanghai, China |
Self-Replicating RNA |
Rona Therapeutics |
Shanghai, China |
RNA Therapeutics Platform |
RVAC Medicines |
Shanghai, China |
mRNA, vaccines, and lipid nanoparticle technologies |
StemiRNA Therapeutics |
Shanghai, China |
mRNA Treatments |
Frontera Therapeutics |
Suzhou, China |
Gene Therapy Development |
Sirnaomics |
Suzhou, China |
RNAi Therapeutics |
Starna Therapeutics |
Suzhou, China |
mRNA vaccine, therapies |
Recbio Technology |
Taizhou, China |
mRNA Covid Vaccine |
Neurophth Therapeutics |
Wuhan, China |
Ophthalmology Gene Therapy |
Viridian Therapeutics |
Boulder, CO |
MicroRNA |
IO Biotech |
Copenhagen, Denmark |
Immuno-Oncology |
SNIPR BIOME |
Copenhagen, Denmark |
CRISPR for microbiome management |
Zealand Pharma |
Soborg, Denmark |
Peptide Drugs |
Valo Therapeutics |
Helsinki, Finland |
Oncolytic Virus, Peptide |
AGTC |
Alachua, FL |
Gene Therapy |
Advanced Innovative Partners |
Surfside, FL |
Breast Cancer Theranostics, Peptide Receptor Radionuclide Therapy |
InnoSkel |
Biot, France |
Therapies for Rare Skeletal Diseases |
Amolyt Pharma |
Ecully, France |
Therapeutic Peptides |
Généthon |
Evry , France |
Gene Therapy |
Transgene |
Illkirch-Graffenstaden, France |
Viral Vector Therapeutics, Gene Therapy |
Axoltis Pharma |
Lyon, France |
Neurological Peptide Drugs |
Tollys |
Lyon, France |
dsRNA Therapy |
Transgene |
Lyon, France |
Viral Vector Therapeutics, Gene Therapy |
Eli Lilly |
Neuilly-sur-Seine, France |
Small Molecules, Biologics |
Lysogene |
Neuilly-sur-Seine, France |
AAV gene therapy technology |
Coave Therapeutics |
Paris, France |
Gene Therapy in Ophthalmology |
EG 427 |
Paris, France |
Pinpoint Gene Therapy |
GenSight Biologics |
Paris, France |
Ophthalmic Gene Therapy |
Inotrem |
Paris, France |
Peptide Therapy |
Invectys |
Paris, France |
DNA Vaccine |
Jalon Therapeutics |
Paris, France |
Cell-Penetrating Peptide |
SparingVision |
Paris, France |
Retinal Gene Therapy Treatments |
Vivet Therapeutics |
Paris, France |
Gene Therapy for Orphan Diseases |
Inotrem |
Vandoeuvre, France |
Peptide Therapy |
Genecure |
Norcross, GA |
Gene Therapy |
Berlin Cures |
Berlin, Germany |
Aptamer for Cardio Indication |
BioNTech |
Berlin, Germany |
mRNA, Vaccines, Biologics |
Silence Therapeutics |
Berlin, Germany |
RNAi |
CureVac |
Frankfurt, Germany |
MRNA treatments |
DiNAQOR |
Hamburg, Germany |
Gene Therapy for Heart Conditions |
Cardior Pharmaceuticals |
Hanover, Germany |
Non-coding RNA based therapeutics |
Pantherna Therapeutics |
Hennigsdorf, Germany |
Nanoparticle Delivery for mRNA drugs |
BioNTech |
Idar-Oberstein, Germany |
mRNA, Vaccines, Biologics |
BioNTech |
Mainz, Germany |
mRNA, Vaccines, Biologics |
Sterna Biologicals & KG |
Marburg, Germany |
Antisense Molecule - DNAzyme |
Ethris |
Planegg, Germany |
MRNA-based therapies, vaccines |
Freeline Therapeutics |
Planegg, Germany |
Protein replacement via Gene Therapy |
ViGeneron |
Planegg, Germany |
Gene Therapy |
CureVac |
Tübingen, Germany |
MRNA treatments |
Exicure |
Chicago, IL |
Spherical Nucleic Acid |
MAIA Biotechnology |
Chicago, IL |
Peptide Cancer Therapies |
Jaguar Gene Therapy |
Lake Forest, IL |
AAV-Based Gene Therapies |
MBX Biosciences |
Carmel, IN |
Hormone Analogues for Rare Endocrine Diseases |
Eli Lilly |
Indianapolis, IN |
Small Molecules, Biologics |
Eli Lilly |
Kinsale, Ireland |
Small Molecules, Biologics |
SpliSense |
Jerusalem, Israel |
Antisense Oligonucleotides |
Eleven Therapeutics |
Tel Aviv, Israel |
Small interfering RNAs with ultra-long durability by utilizing high throughput combinatorial chemistry and AI |
Altheia Science |
Milan, Italy |
Cell & Gene Therapy for Autoimmune Disorders |
Holostem Tarapie Avanzate |
Modena, Italy |
Cell & Gene Therapy |
Eli Lilly |
Sesto Fiorentino, Italy |
Small Molecules, Biologics |
Kither Biotech |
Torino, Italy |
Therapies for the treatment of rare pulmonary diseases |
WaVe Life Sciences |
Kagoshima, Japan |
Stereopure oligonucleotides |
Gene Therapy Research Institute (GTRI) |
Kanagawa, Japan |
Gene Therapy |
Oncotherapy Science |
Kawasaki, Japan |
Small Molecule, peptides, antibody therapies, contract analytical |
Luxna Biotech |
Osaka, Japan |
Oligonucleotide Therapeutics |
Epsilon Molecular Engineering |
Saitama, Japan |
Heavy chain single domain antibodies |
Ribomic |
Tokyo , Japan |
Aptamers |
TAGCyx Biotechnologies |
Tokyo, Japan |
Oligonucleotide Drug Discovery Platform |
Biorchestra |
Daejeon, Korea |
Novel RNA-based Therapeutics |
GenKOre |
Daejeon, Korea |
Gene-editing therapies |
OliPass |
Gyeonggi, Korea |
Peptide nucleic acid derivatives |
OliX Pharmaceuticals |
Gyeonggi, Korea |
RNAi Treatments |
Genexine |
Seongnam, Korea |
Biologics, DNA Plasmid Vaccine |
Aston Sci. |
Seoul, Korea |
Therapeutic cancer vaccines and proteostasis modulators |
Curamys |
Seoul, Korea |
Stem Cell Fusion Technology |
GenKOre |
Seoul, Korea |
Gene-editing therapies |
Helixmith |
Seoul, Korea |
plasmid DNA based gene therapy |
Kolon Life Science |
Seoul, Korea |
Cell & Gene Therapy, APIs |
MDimune |
Seoul, Korea |
Drug Delivery Based on Cell-Derived Vesicles |
Apellis Pharmaceuticals |
Crestwood, KY |
Cyclic peptide analog |
Frontera Therapeutics |
Bedford, MA |
Gene Therapy Development |
Homology Medicines |
Bedford, MA |
Gene-editing via homologous recombination |
Stoke Therapeutics |
Bedford, MA |
Antisense Oligonucleotide Medicines |
Aera Therapeutics |
Boston, MA |
Genetic Medicines |
Aileron Therapeutics |
Boston, MA |
Perpetually Active Peptides |
Akouos |
Boston, MA |
Gene Therapy for Hearing Disorders |
Ampersand Biomedicines |
Boston, MA |
AND-Body Therapeutica |
Ascidian Therapeutics |
Boston, MA |
Mutated exon replacement |
Atalanta Therapeutics |
Boston, MA |
RNAi therapeutics |
Cell BioEngines |
Boston, MA |
Cell-based Immunotherapies |
CureVac |
Boston, MA |
MRNA treatments |
Inozyme Pharma |
Boston, MA |
Enzyme Replacement Therapy |
Kelonia Therapeutics |
Boston, MA |
in vivo CAR T Gene Therapy |
Orchard Therapeutics |
Boston, MA |
Ex-vivo autologous hematopoietic stem cell gene therapy |
Rhythm Pharmaceuticals |
Boston, MA |
Peptide Therapeutics |
Strand Therapeutics |
Boston, MA |
Gene Therapy |
STRM.BIO |
Boston, MA |
Extracellular vesicles (EVs) to deliver gene therapies |
TransCode Therapeutics |
Boston, MA |
RNA Delivery, Small Molecule |
Transgene |
Boston, MA |
Viral Vector Therapeutics, Gene Therapy |
AGTC |
Cambridge, MA |
Gene Therapy |
Alltrna |
Cambridge, MA |
tRNA therapies |
Alnylam Pharmaceuticals |
Cambridge, MA |
RNAi |
Apic Bio |
Cambridge, MA |
Gene Therapy |
AVROBIO |
Cambridge, MA |
Cellular & Gene Therapies |
Axcella Therapeutics |
Cambridge, MA |
Amino acid mediated therapeutics |
BioNTech |
Cambridge, MA |
mRNA, Vaccines, Biologics |
Biorchestra |
Cambridge, MA |
Novel RNA-based Therapeutics |
bluebird bio |
Cambridge, MA |
Gene Therapy, Cellular Extraction & Reintroduction |
Dicerna Pharmaceuticals |
Cambridge, MA |
RNAi |
Eli Lilly |
Cambridge, MA |
Small Molecules, Biologics |
Generation Bio |
Cambridge, MA |
Gene Therapy |
hC Bioscience |
Cambridge, MA |
tRNA-based Therapeutics |
Helix Nanotechnologies |
Cambridge, MA |
DNA Therapy |
Hunterian Medicine |
Cambridge, MA |
CRISPR-based drug discovery |
Intergalactic Therapeutics |
Cambridge, MA |
Non-viral Gene Therapy |
Korro Bio |
Cambridge, MA |
RNA-editing Drugs |
Laronde |
Cambridge, MA |
Plasmid RNA Therapeutics |
Lytica Therapeutics |
Cambridge, MA |
Antimicrobial peptide Design |
Moderna Therapeutics |
Cambridge, MA |
RNA Therapies |
Obsidian Therapeutics |
Cambridge, MA |
Cell & Gene Therapies |
Omega Therapeutics |
Cambridge, MA |
Gene Editing |
Orbital Therapeutics |
Cambridge, MA |
RNA technology (not RNAi) |
Orna Therapeutics |
Cambridge, MA |
oRNA, Delivery |
ProQR Therapeutics |
Cambridge, MA |
Oligonucleotide Therapy |
Regel Therapeutics |
Cambridge, MA |
AAV gene delivery |
Repertoire Immune Medicines |
Cambridge, MA |
Cell & Peptide-Based Therapies |
SalioGen Therapeutics |
Cambridge, MA |
Gene Therapy Platform Technology |
SmartPharm Therapeutics |
Cambridge, MA |
Production of biologics within patients via gene therapy |
Solid Biosciences |
Cambridge, MA |
Gene Therapy, Devices, Biologics, Small Molecules all for DMD |
Sumitomo Pharma Oncology |
Cambridge, MA |
RNAi, Small Molecules |
Tevard Biosciences |
Cambridge, MA |
tRNA-based Gene Therapies |
Ultragenyx Pharmaceutical |
Cambridge, MA |
Small Molecules, Biologics |
Verve Therapeutics |
Cambridge, MA |
Gene-editing Treatments |
Vigeo Therapeutics |
Cambridge, MA |
Biologics for Cancer |
Voyager Therapeutics |
Cambridge, MA |
AAV capsid Gene Therapy |
WaVe Life Sciences |
Cambridge, MA |
Stereopure oligonucleotides |
Bicycle Therapeutics |
Lexington, MA |
Peptides |
Carbon Biosciences |
Lexington, MA |
Gene Therapy |
Exegenesis Bio |
Lexington, MA |
Gene Therapy |
LogicBio Therapeutics |
Lexington, MA |
Gene Therapy |
uniQure |
Lexington, MA |
Gene Therapy |
Alcyone Therapeutics |
Lowell, MA |
Gene Therapy |
Phio Pharmaceuticals |
Marlborough, MA |
RNAi |
RVAC Medicines |
Medford, MA |
mRNA, vaccines, and lipid nanoparticle technologies |
Avenge Bio |
Natick, MA |
Cell & Gene Therapies |
Remedium Bio |
Needham, MA |
Gene Therapy |
Moderna Therapeutics |
Norwood, MA |
RNA Therapies |
Affinia Therapeutics |
Waltham, MA |
Gene Delivery |
Apellis Pharmaceuticals |
Waltham, MA |
Cyclic peptide analog |
Viridian Therapeutics |
Waltham, MA |
MicroRNA |
Selecta Biosciences |
Watertown, MA |
Immunogenicity Prevention in Biologic and Enzyme Therapy |
Sonata Therapeutics |
Watertown, MA |
Small Molecules, Gene Therapy |
SanegeneBio |
Woburn, MA |
siRNA Drug Discovery |
Ultragenyx Pharmaceutical |
Woburn, MA |
Small Molecules, Biologics |
Leal Therapeutics |
Worcester, MA |
CNS Therapies |
Mustang Bio |
Worcester, MA |
Immunotherapies |
Zata Pharmaceuticals |
Worcester, MA |
RNA, DNA Therapeutics |
Ibex Biosciences |
Cumberland, MD |
Biologics, Cell Therapy, Gene Therapy |
BioNTech |
Gaithersburg , MD |
mRNA, Vaccines, Biologics |
miRecule |
Gaithersburg, MD |
microRNA Therapeutics for Cancer |
RNAimmune |
Gaithersburg, MD |
mRNA therapies |
Sirnaomics |
Gaithersburg, MD |
RNAi Therapeutics |
Precigen |
Germantown, MD |
Cell & Gene Therapy |
American Gene Technologies |
Rockville, MD |
Gene Therapy and Immunotherapy Company. Lentiviral Vector Platform and Indication-Specific Technologies. Lead Therapeutics for an HIV Cure, Liver Cancer Cure, and PKU therapy |
ReGenX Biosciences |
Rockville, MD |
Gene Therapy, Biologics |
Rithim Biologics |
Woodbinw, MD |
Gene Therapy for Tachycardias |
Eli Lilly |
San José, Mexico |
Small Molecules, Biologics |
ONL Therapeutics |
Ann Arbor, MI |
Small molecule peptide |
Vir Biotechnology |
St. Louis, MO |
Infectious disease therapies |
Atsena Therapeutics |
Durham, NC |
Gene Therapy |
bluebird bio |
Durham, NC |
Gene Therapy, Cellular Extraction & Reintroduction |
Fennec Pharmaceuticals |
Durham, NC |
Small Molecules, Cyclic Peptides |
Pfizer |
Durham, NC |
Small Molecules, Vaccines, Biologics |
StrideBio |
Durham, NC |
Antibody-Evading Gene Therapy |
Tune Therapeutics |
Durham, NC |
Epigenetic modification to modulate gene expression |
Kriya Therapeutics |
Morrisville, NC |
Gene Therapy |
uniQure |
Amsterdam, Netherlands |
Gene Therapy |
VectorY |
Amsterdam, Netherlands |
Vectorized Antibodies |
Amarna Therapeutics |
Leiden, Netherlands |
Viral Gene Delivery Platform |
Amylon Therapeutics |
Leiden, Netherlands |
RNA-based therapies |
Hybridize Therapeutics |
Leiden, Netherlands |
RNA treatments for kidney disease |
ProQR Therapeutics |
Leiden, Netherlands |
Oligonucleotide Therapy |
Vico Therapeutics |
Leiden, Netherlands |
Oligonucleotide based RNA modulating therapeutics |
Chondropeptix |
Maastricht, Netherlands |
Peptide for cartilage improvement |
InteRNA Technologies |
Nijmegen, Netherlands |
MiRNA Therapeutics |
DegenRx |
Tilburg, Netherlands |
Gene Therapy, Antibodies |
Treeway |
Tilburg, Netherlands |
Small Molecules, Gene Therapy |
InteRNA Technologies |
Utrecht, Netherlands |
MiRNA Therapeutics |
IVERIC Bio |
Cranbury, NJ |
Aptamers, Biologics |
Rocket Pharmaceuticals |
Cranbury, NJ |
Gene Therapies |
Ceptur Therapeutics |
Hillsborough, NJ |
U1 Adaptor Technology for RNA Therapeutics |
Silence Therapeutics |
Hoboken, NJ |
RNAi |
EOM Pharmaceuticals |
Montvale, NJ |
Peptide-nucleic Acid Solutions |
Nykode Therapeutics |
Oslo, Norway |
Therapeutic DNA Vaccine |
Sapience Therapeutics |
Harrison, NY |
Peptide-based Therapies for cancers |
Apertura Gene Therapy |
New York, NY |
AAV vectors for Gene Therapy |
Lexeo Therapeutics |
New York, NY |
Gene Therapy |
Neurogene |
New York, NY |
Genetic Therapies |
Oncogenuity |
New York, NY |
Oligonucleotide platform for the treatment of genetically driven cancers |
Prevail Therapeutics |
New York, NY |
AAV-based gene therapies |
iCell Gene Therapeutics |
Stony Brook, NY |
Gene Therapy for Cancer |
Abeona Therapeutics |
Cleveland, OH |
Therapies for Sanfilippo (SF) Syndrome Type A and Type B. |
ExonanoRNA |
Columbus, OH |
RNA nanoparticles, therapies |
Deep Genomics |
Toronto, ON |
AI-discovery, Oligonucleotide Therapies |
Vir Biotechnology |
Portland, OR |
Infectious disease therapies |
SwanBio Therapeutics |
Bala Cynwyd, PA |
Gene Therapy |
Code Biotherapeutics |
Hatfield, PA |
DNA-based Gene Therapy Vector |
Gyroscope Therapeutics |
King of Prussia, PA |
Gene Therapy |
NanoCell Therapeutics |
King of Prussia, PA |
Gene Therapy |
Exegenesis Bio |
Lower Gwynedd, PA |
Gene Therapy |
Aro Biotherapeutics |
Philadelphia, PA |
Protein Scaffolds, Antisense Oligonucleotide |
Chimeron Bio |
Philadelphia, PA |
Cancer Immunotherapy |
Interius BioTherapeutics |
Philadelphia, PA |
Novel methods for in vivo cell-specific gene delivery |
Longevity Biotech |
Philadelphia, PA |
Synthetic Peptides |
NeuExcell Therapeutics |
Philadelphia, PA |
Gene Therapy for Neural Regeneration & Repair |
Opus Genetics |
Philadelphia, PA |
Ophthalmology Gene Therapy |
Passage Bio |
Philadelphia, PA |
Gene Therapy |
SparingVision |
Philadelphia, PA |
Retinal Gene Therapy Treatments |
Spark Therapeutics |
Philadelphia, PA |
Singe Dose Gene Therapy |
Spirovant Sciences |
Philadelphia, PA |
Gene Therapy - Lung Diseases |
Krystal Biotech |
Pittsburgh, PA |
Gene Therapy |
Peptilogics |
Pittsburgh, PA |
Peptide Therapeutics |
Geneos Therapeutics |
Plymouth Meeting, PA |
Plasmid-based Neoantigen-targeted Cancer Therapies |
Inovio Pharmaceuticals |
Plymouth Meeting, PA |
DNA Vaccines |
Arbutus Biopharma |
Warminster, PA |
RNAi |
Windtree Therapeutics |
Warrington, PA |
Peptides |
XyloCor Therapeutics |
Wayne, PA |
Gene Therapy |
Verrica Pharmaceuticals |
West Chester, PA |
Topical therapies |
ExploRNA Therapeutics |
Warsaw, Poland |
mRNA Therapies |
Eli Lilly |
Carolina, PR |
Recombinant Insulin |
Eli Lilly |
Mayaguez, PR |
Small Molecules, Biologics |
ExCellThera |
Montréal, QC |
Growing blood stem cells for therapeutic use |
Feldan Therapeutics |
Quebec City, QC |
Peptide-based Intracellular Delivery Technology |
Xequel Bio |
Mount Pleasant, SC |
Peptide for Injury Healing |
Carmine Therapeutics |
Singapore, Singapore |
Medicines based on red blood cell extracellular vesicles (RBCEVs), for the delivery of novel therapeutic modalities that include nucleic acids |
Nuevocor |
Singapore, Singapore |
AAV-based gene therapy |
Cargene |
Singapore , Singapore |
Nucleic Acid Therapeutics |
Juniper Biologics |
Singapore , Singapore |
Small Molecules, Cell Therapy, Gene Therapy |
RVAC Medicines |
Singapore , Singapore |
mRNA, vaccines, and lipid nanoparticle technologies |
Eli Lilly |
Alcobendas, Spain |
Small Molecules, Biologics |
Esteve |
Barcelona, Spain |
Small Molecules, Gene Therapy |
Peptomyc |
Barcelona, Spain |
Cell Penetrating Peptides |
Sylentis |
Madrid, Spain |
RNAi Treatments |
Cyxone |
Malmö, Sweden |
Immunomodulating cyclotides for the treatment of autoimmune diseases |
InDex Pharmaceuticals |
Solna, Sweden |
DNA-Based Drugs, Diagnostics |
Versameb |
Basel, Switzerland |
RNA Therapeutics |
Vir Biotechnology |
Bellinzona, Switzerland |
Infectious disease therapies |
Antion Biosciences |
Geneva, Switzerland |
Gene & Cell Therapy |
HAYA Therapeutics |
Lausanne, Switzerland |
RNA-based, RNA-targeting Fibrotic Therapies |
Anjarium Biosciences |
Schlieren, Switzerland |
Non-viral Gene Therapy |
DiNAQOR |
Schlieren, Switzerland |
Gene Therapy for Heart Conditions |
Redbiotec |
Schlieren, Switzerland |
Various Biologic Modalities |
Alnylam Pharmaceuticals |
Zug, Switzerland |
RNAi |
Genprex |
Austin, TX |
Immunogene Therapy |
Bio-Path Holdings |
Bellaire, TX |
Antisense DNA therapeutics |
Nanoscope Therapeutics |
Dallas, TX |
AAV-delivered opsin |
ReCode Therapeutics |
Dallas, TX |
Nucleic Acid Therapeutic Delivery |
Taysha Gene Therapies |
Dallas, TX |
Adeno-associated virus gene therapies |
Vaxxinity |
Dallas, TX |
Endobody Vaccines, Synthetic Peptides Vaccine |
Xequel Bio |
Fort Worth, TX |
Peptide for Injury Healing |
Neurogene |
Houston, TX |
Genetic Therapies |
Eli Lilly |
Basingstoke, UK |
Small Molecules, Biologics |
Bicycle Therapeutics |
Cambridge, UK |
Peptides |
Eleven Therapeutics |
Cambridge, UK |
Small interfering RNAs with ultra-long durability by utilizing high throughput combinatorial chemistry and AI |
Transine Therapeutics |
Cambridge, UK |
IncRNA |
VaxEquity |
Cambridge, UK |
Self-amplifying RNA |
Causeway Therapeutics |
Glasgow, UK |
microRNA |
|
Hampton, UK |
Touchlight DNA Services provide rapid, enzymatic GMP DNA manufacturing for advanced therapeutics | antibiotic free DNA vector | fast turnaround for GMP production | doggybone DNA |
AviadoBio |
London, UK |
Gene Therapies for neurodegenerative |
DiNAQOR |
London, UK |
Gene Therapy for Heart Conditions |
Gyroscope Therapeutics |
London, UK |
Gene Therapy |
MeiraGTx |
London, UK |
Gene Therapy |
MiNA Therapeutics |
London, UK |
Small activating RNA |
Orchard Therapeutics |
London, UK |
Ex-vivo autologous hematopoietic stem cell gene therapy |
Poolbeg Pharma |
London, UK |
Developing drugs to sell off |
Purespring Therapeutics |
London, UK |
Gene Therapy for Kidney Disease |
Silence Therapeutics |
London, UK |
RNAi |
Alnylam Pharmaceuticals |
Maidenhead, UK |
RNAi |
Ochre Bio |
Oxford, UK |
siRNA liver drugs |
Oxford Biomedica |
Oxford, UK |
Gene-based Medicines |
Valo Therapeutics |
Oxford, UK |
Oncolytic Virus, Peptide |
Freeline Therapeutics |
Stevenage, UK |
Protein replacement via Gene Therapy |
Sumitomo Pharma Oncology |
Lehi, UT |
RNAi, Small Molecules |
PEEL Therapeutics |
Salt Lake City, UT |
Nature-inspired Cancer Therapies |
AltPep |
Seattle, WA |
Alternating Peptides for Neurological Diseases |
bluebird bio |
Seattle, WA |
Gene Therapy, Cellular Extraction & Reintroduction |
Sana Biotechnology |
Seattle, WA |
Cell & Gene Therapies |
Shape Therapeutics |
Seattle, WA |
RNA-editing gene therapy |
Tune Therapeutics |
Seattle, WA |
Epigenetic modification to modulate gene expression |
Arrowhead Pharmaceuticals |
Madison, WI |
RNAi |
Nimble Therapeutics |
Madison, WI |
Photoprotected Amino Acids |